SMA drug risdiplam shows nerve repair promise in new study

NCT ID NCT05219487

First seen Feb 24, 2026 · Last updated May 14, 2026 · Updated 15 times

Summary

This study looked at 18 adults with spinal muscular atrophy (SMA) who had taken the oral medication risdiplam for at least one year. Researchers measured how well nerves and muscles communicate using electrical tests and walking tests. The goal was to see if risdiplam improves nerve-muscle junction function beyond what is already known.

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Contacts and locations

Locations

  • The Ohio State University Wexner Medical Center

    Columbus, Ohio, 43210, United States

Conditions

Explore the condition pages connected to this study.