SMA drug effects under the microscope: new study launches

NCT ID NCT06532474

First seen Nov 01, 2025 · Last updated Jun 16, 2026 · Updated 26 times

Summary

This study watches how spinal muscular atrophy (SMA) drugs work on muscles and nerves in 24 children and teens (ages 5-20) with SMA types 2 and 3. Researchers use MRI scans, strength tests, and blood samples to track changes over 12 months. The goal is to better understand how treatments affect the body, not to test a new drug.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • St. Jude Children's Research Hospital

    RECRUITING

    Memphis, Tennessee, 38105, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.