Scientists peek inside muscles to see how SMA drugs really work
NCT ID NCT06532474
First seen Nov 01, 2025 · Last updated Apr 29, 2026 · Updated 19 times
Summary
This study watches how spinal muscular atrophy (SMA) drugs affect muscles and nerves in 24 children and teens aged 5 to 20 with SMA types 2 and 3. Researchers use MRI scans, blood tests, and muscle function tests to track changes over 12 months. The goal is to better understand how treatments work, not to test a new drug.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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St. Jude Children's Research Hospital
RECRUITINGMemphis, Tennessee, 38105, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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