Scientists probe why SMA patients still feel worn out despite treatment

NCT ID NCT06955897

Summary

This study aims to better understand how people with Spinal Muscular Atrophy experience physical fatigue during their daily activities while receiving nusinersen treatment. Researchers will follow 45 adolescents and adults who have been on stable nusinersen dosing for at least 6 months, using a new questionnaire specifically designed for SMA patients. The goal is to measure how fatigue changes before and after treatment doses and learn more about this persistent symptom.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for SPINAL MUSCULAR ATROPHY are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Columbia University Irving Medical Center

    RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.