New combo pill aims to boost CF treatment in small safety study

NCT ID NCT07108153

First seen Oct 31, 2025 · Last updated May 13, 2026 · Updated 19 times

Summary

This early study tests whether adding an experimental drug called SION-719 to the standard CF medicine Trikafta is safe and tolerable. Sixteen adults with cystic fibrosis who have two copies of the F508del mutation will receive either SION-719 or a placebo alongside their usual Trikafta. Researchers will monitor side effects, measure sweat chloride levels, and track drug concentrations in the blood.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Boston Children's Hospital

    Boston, Massachusetts, 02115, United States

  • Columbia University

    New York, New York, 10032, United States

  • Gold Coast University Hospital

    Southport, Queensland, 4215, Australia

  • Johns Hopkins

    Baltimore, Maryland, 21205, United States

  • Medical University of South Carolina

    Charleston, South Carolina, 29425, United States

  • Monash University

    Melbourne, Victoria, 3004, Australia

  • National Jewish Health

    Denver, Colorado, 80206, United States

  • New York Medical College

    Hawthorne, New York, 10532, United States

  • Royal Prince Alfred Hospital

    Camperdown, New South Wales, 2050, Australia

  • University Hospital of Cleveland

    Cleveland, Ohio, 44106, United States

  • University of Iowa

    Iowa City, Iowa, 52242, United States

  • University of Washington

    Seattle, Washington, 98195, United States

  • Washington University

    St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.