Gene therapy trial aims to help boys with duchenne walk stronger
NCT ID NCT07160634
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests a one-time gene therapy called SGT-003 in 80 boys with Duchenne muscular dystrophy who can still walk. The goal is to see if it helps them move better, like standing up faster and climbing stairs. Participants will receive either the therapy or a placebo first, then switch, and be followed for at least 5 years.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Arkansas Children's Hospital
NOT_YET_RECRUITINGLittle Rock, Arkansas, 72202, United States
Contact Email: •••••@•••••
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BC Children's Hospital
RECRUITINGVancouver, British Columbia, Canada
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital of the King's Daughters
NOT_YET_RECRUITINGNorfolk, Virginia, 23510, United States
Contact Email: •••••@•••••
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Neurology Rare Disease Center
NOT_YET_RECRUITINGFlower Mound, Texas, 75082, United States
Contact Email: •••••@•••••
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The Children's Hospital of Westmead
RECRUITINGSydney, New South Wales, Australia
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact