Rabbit-Milk clotting drug tested for hemophilia bleeds

NCT ID NCT04647227

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study is testing the safety of a drug called SEVENFACT, a clotting factor made from the milk of genetically modified rabbits, in people aged 12 and older with hemophilia A or B who have inhibitors. The drug is already approved for treating bleeding episodes, and this trial will monitor side effects in 55 participants across the US. It is an open-label study, meaning everyone knows they are getting the drug.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
SEVENFACT (a clotting factor made from rabbit milk)
What this could lead to
If successful, this could confirm that SEVENFACT is a safe option to control bleeding episodes in people with hemophilia who have inhibitors.
What could go wrong
This is a small, early-phase safety study (55 people) with no comparison group, so it cannot prove effectiveness. Side effects like allergic reactions or blood clots are possible.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Arizona Hemophilia and Thrombosis Center at Phoenix Children's Hospital

    COMPLETED

    Phoenix, Arizona, 85016, United States

  • Arkansas Center for Bleeding Disorders

    RECRUITING

    Little Rock, Arkansas, 72202, United States

  • Arnold Palmer Hospital for Children - The Haley Center for Children's Cancer and Blood Disorders

    COMPLETED

    Orlando, Florida, 32806, United States

  • Brody School of Medicine at East Carolina University

    NOT_YET_RECRUITING

    Greenville, North Carolina, 27834, United States

  • Center for Bleeding and Clotting Disorders, University of Minnesota

    NOT_YET_RECRUITING

    Minneapolis, Minnesota, 55455, United States

  • Children's Hospital of Michigan

    RECRUITING

    Detroit, Michigan, 48201, United States

  • Children's National Hemophilia Center

    COMPLETED

    Washington D.C., District of Columbia, 20010, United States

  • Gulf States Hemophilia and Thrombophilia Center-University of Texas Health Science Center @Houston

    RECRUITING

    Houston, Texas, 77030, United States

  • Hemophilia of Georgia Center for Bleeding and Clotting Disorders of Emory, Adult Division

    RECRUITING

    Atlanta, Georgia, 31404, United States

  • Henry Ford Health System

    RECRUITING

    Detroit, Michigan, 48202, United States

  • Kansas City Regional Hemophilia Center

    RECRUITING

    Kansas City, Missouri, 64108, United States

  • MSU Center for Bleeding and Clotting Disorders

    RECRUITING

    Lansing, Michigan, 48912, United States

  • Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center

    RECRUITING

    Boston, Massachusetts, 02114, United States

  • Mayo Comprehensive Hemophilia Center

    COMPLETED

    Rochester, Minnesota, 55905, United States

  • Northwell Health, Long Island Jewish

    RECRUITING

    New Hyde Park, New York, 11040, United States

  • Oklahoma Center for Bleeding and Clotting Disorders

    RECRUITING

    Oklahoma City, Oklahoma, 73104, United States

  • Orthopaedic Institute for Children

    RECRUITING

    Los Angeles, California, 90007, United States

  • University Hospitals Health System Cleveland

    RECRUITING

    Cleveland, Ohio, 44106, United States

  • University of California at Davis UC Davis Hemostasis and Thrombosis Center

    RECRUITING

    Sacramento, California, 95817, United States

  • Vanderbilt University Medical Center

    RECRUITING

    Nashville, Tennessee, 37212, United States

  • Willett Children's Hospital at Memorial University Medical Center

    RECRUITING

    Savannah, Georgia, 31404, United States

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