New hope for shrinking painful tumors in adults with rare genetic disorder

NCT ID NCT04924608

Summary

This global study is testing whether the drug selumetinib can shrink painful, inoperable tumors in adults with Neurofibromatosis Type 1 (NF1). About 145 participants will be randomly assigned to receive either selumetinib or a placebo to see which is better at reducing tumor size and relieving chronic pain. The main goal is to see if the drug leads to a confirmed partial or complete shrinkage of the target tumor by the end of the treatment period.

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Contacts and locations

Locations

  • Research Site

    Gainesville, Florida, 32610, United States

  • Research Site

    Rockville, Maryland, 20852, United States

  • Research Site

    St Louis, Missouri, 63156, United States

  • Research Site

    Commack, New York, 11725, United States

  • Research Site

    Melbourne, 3000, Australia

  • Research Site

    St Leonards, 2065, Australia

  • Research Site

    Porto Alegre, 90035-903, Brazil

  • Research Site

    Ribeirão Preto, 14051-140, Brazil

  • Research Site

    São Paulo, 045202-001, Brazil

  • Research Site

    Toronto, Ontario, M5G 2C4, Canada

  • Research Site

    Montreal, Quebec, H4A 3J1, Canada

  • Research Site

    Beijing, 100070, China

  • Research Site

    Beijing, 100730, China

  • Research Site

    Guangzhou, 510060, China

  • Research Site

    Shenyang, 110001, China

  • Research Site

    Créteil, 94000, France

  • Research Site

    Lyon, 69008, France

  • Research Site

    Toulouse, 31059, France

  • Research Site

    Hamburg, 20246, Germany

  • Research Site

    Tübingen, 72076, Germany

  • Research Site

    Würzburg, 97080, Germany

  • Research Site

    Milan, 20133, Italy

  • Research Site

    Naples, 80131, Italy

  • Research Site

    Roma, 00165, Italy

  • Research Site

    Minatoku, 105-8471, Japan

  • Research Site

    Nagoya, 466-8560, Japan

  • Research Site

    Shinjuku-ku, 160-8582, Japan

  • Research Site

    Bydgoszcz, 85-094, Poland

  • Research Site

    Moscow, 115522, Russia

  • Research Site

    Moscow, 125412, Russia

  • Research Site

    Badalona, 08916, Spain

  • Research Site

    Madrid, 28041, Spain

  • Research Site

    London, SE1 9RT, United Kingdom

  • Research Site

    Manchester, M20 4BX, United Kingdom

Conditions

Explore the condition pages connected to this study.