Tracking a lifeline: Real-World look at drug for Kids' debilitating tumors

NCT ID NCT06175637

Summary

This study aims to understand how well the drug selumetinib works and how safe it is for children in China with a genetic condition called NF1, which causes painful, inoperable nerve tumors. It will follow about 80-100 children already receiving this approved treatment in real-world hospital settings for up to two years. The goal is to gather practical information on how the drug helps control tumor growth and manages symptoms like pain in everyday clinical practice.

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Contacts and locations

Locations

  • Research Site

    Beijing, Beijing Municipality, China

  • Research Site

    Chongqing, Chongqing Municipality, China

  • Research Site

    Lanzhou, Gansu, China

  • Research Site

    Guangzhou, Guangdong, China

  • Research Site

    Shenzhen, Guangdong, China

  • Research Site

    Nanning, Guangxi, China

  • Research Site

    Guiyang, Guizhou, China

  • Research Site

    Shijiazhuang, Hebei, China

  • Research Site

    Zhengzhou, Henan, China

  • Research Site

    Wuhan, Hubei, China

  • Research Site

    Changsha, Hunan, China

  • Research Site

    Nanjing, Jiangsu, China

  • Research Site

    Suzhou, Jiangsu, China

  • Research Site

    Nanchang, Jiangxi, China

  • Research Site

    Shenyang, Liaoning, China

  • Research Site

    Jinan, Shandong, China

  • Research Site

    Shanghai, Shanghai Municipality, China

  • Research Site

    Taiyuan, Shanxi, China

  • Research Site

    Xi’an, Shanxi, China

  • Research Site

    Chengdu, Sichuan, China

  • Research Site

    Tianjin, Tianjin Municipality, China

  • Research Site

    Kunming, Yunnan, China

  • Research Site

    Hangzhou, Zhejiang, China

  • Research Site

    Wenzhou, Zhejiang, China

  • Research Site

    Nanjing, China

Conditions

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