New hope for NF1 patients: drug trial targets painful tumors

NCT ID NCT04924608

First seen Nov 01, 2025 · Last updated Apr 25, 2026 · Updated 31 times

Summary

This study tests a drug called selumetinib in adults with neurofibromatosis type 1 (NF1) who have painful nerve tumors that cannot be removed by surgery. The goal is to see if the drug can shrink these tumors and reduce pain. About 145 participants worldwide will receive either selumetinib or a placebo, and their tumor size and pain levels will be tracked over time.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for NEUROFIBROMATOSIS 1 are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Research Site

    Gainesville, Florida, 32610, United States

  • Research Site

    Rockville, Maryland, 20852, United States

  • Research Site

    St Louis, Missouri, 63156, United States

  • Research Site

    Commack, New York, 11725, United States

  • Research Site

    Melbourne, 3000, Australia

  • Research Site

    St Leonards, 2065, Australia

  • Research Site

    Porto Alegre, 90035-903, Brazil

  • Research Site

    Ribeirão Preto, 14051-140, Brazil

  • Research Site

    São Paulo, 045202-001, Brazil

  • Research Site

    Toronto, Ontario, M5G 2C4, Canada

  • Research Site

    Montreal, Quebec, H4A 3J1, Canada

  • Research Site

    Beijing, 100070, China

  • Research Site

    Beijing, 100730, China

  • Research Site

    Guangzhou, 510060, China

  • Research Site

    Shenyang, 110001, China

  • Research Site

    Créteil, 94000, France

  • Research Site

    Lyon, 69008, France

  • Research Site

    Toulouse, 31059, France

  • Research Site

    Hamburg, 20246, Germany

  • Research Site

    Tübingen, 72076, Germany

  • Research Site

    Würzburg, 97080, Germany

  • Research Site

    Milan, 20133, Italy

  • Research Site

    Naples, 80131, Italy

  • Research Site

    Roma, 00165, Italy

  • Research Site

    Minatoku, 105-8471, Japan

  • Research Site

    Nagoya, 466-8560, Japan

  • Research Site

    Shinjuku-ku, 160-8582, Japan

  • Research Site

    Bydgoszcz, 85-094, Poland

  • Research Site

    Moscow, 115522, Russia

  • Research Site

    Moscow, 125412, Russia

  • Research Site

    Badalona, 08916, Spain

  • Research Site

    Madrid, 28041, Spain

  • Research Site

    London, SE1 9RT, United Kingdom

  • Research Site

    Manchester, M20 4BX, United Kingdom

Conditions

Explore the condition pages connected to this study.