New hope for kids with hemophilia: can SCT800 stop bleeds before they start?

NCT ID NCT07437404

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This study is testing a drug called SCT800, a lab-made clotting factor, to prevent bleeding episodes in 36 boys with severe hemophilia A who have never been treated before. Participants receive regular infusions of SCT800, and researchers will monitor how many bleeding events occur and whether the body develops antibodies that could block the treatment. The goal is to see if this approach is safe and effective for long-term prevention.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

SCT800 (a recombinant factor VIII replacement therapy)

What this could lead to

If successful, this could provide a safe and effective preventive treatment option for children with severe hemophilia A who have not yet received any factor VIII therapy.

What could go wrong

This is a small, open-label study with no control group, so results may be less reliable. There is a risk of developing inhibitors (antibodies) that block the treatment's effect, a known complication in previously untreated patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

hemophilia A severe hemophilia A

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Beijing children's hospital

    RECRUITING

    Beijing, Beijing Municipality, 000000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••