New pill for duchenne MD enters Mid-Stage trial in young boys
NCT ID NCT07287189
First seen Jun 27, 2026 · Last updated Aug 14, 2026 · Updated 7 times
Summary
This study tests an oral drug called SAT-3247 in 51 boys aged 7 to 10 with Duchenne muscular dystrophy who can still walk. The goal is to find the best dose, check safety, and see if it helps muscle strength. Participants take the drug or a placebo for 12 weeks, and all continue their usual steroid treatment.
This is an AI summary of the original study and may miss details. Read our disclaimer.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for DMD are added.
By submitting, you agree to our Terms of use
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Locations
-
Children's Hospital Eastern Ontario
RECRUITINGOttawa, Ontario, K1H8L1, Canada
-
Children's Hospital at Westmead
RECRUITINGWestmead, New South Wales, 2145, Australia
-
Clinic of Neurology and Psychiatry for Children and Youth
NOT_YET_RECRUITINGBelgrade, Serbia, 11000, Serbia
-
Colorado Children's
RECRUITINGAurora, Colorado, 80045, United States
-
Great Ormond Street
RECRUITINGLondon, UK, WC1N 3JH, United Kingdom
-
Hospital Infantil i Hospital de la Dona
RECRUITINGBarcelona, 08035, Spain
-
Hospital Universitario Donostia
NOT_YET_RECRUITINGDonostia / San Sebastian, Basque Country, 20014, Spain
-
Hospital Universitario y Politécnico La Fe
RECRUITINGValencia, Valencia, 46026, Spain
-
Hôpital De La Citadelle (CHR)
RECRUITINGLiège, Liège, 4000, Belgium
-
Instytut Centrum Zdrowia Matki Polki
RECRUITINGLodz, Łódź Voivodeship, 93-338, Poland
-
Klinika Neurologii Rozwojowej Uniwersyteckie
RECRUITINGGdansk, Pomeranian Voivodeship, 80-952, Poland
-
Lurie Children's
RECRUITINGChicago, Illinois, 60611, United States
-
Mother and Child Health Care Institute
RECRUITINGBelgrade, Serbia, 11070, Serbia
-
Nationwide Children's Hospital
RECRUITINGColumbus, Ohio, 43205, United States
-
Royal Children's Hospital Melbourne
RECRUITINGMelbourne, Victoria, 3052, Australia
-
Seattle Children's
RECRUITINGSeattle, Washington, 98105, United States
-
UMass Memorial Medical Center
RECRUITINGWorcester, Massachusetts, 01655, United States
-
UZ Gent
RECRUITINGGhent, Oost-Vlaanderen, 9000, Belgium
-
University Children's Clinic Tirsova
NOT_YET_RECRUITINGBelgrade, Serbia, 11000, Serbia
-
University of California Los Angeles
RECRUITINGLos Angeles, California, 90095, United States
-
Washington University
RECRUITINGSt Louis, Missouri, 63110, United States
Contact Email: •••••@•••••
More trials for these conditions
Other studies related to the condition(s) this trial covers.
- Can a lower steroid dose preserve strength in young boys with DMD?
- Can MRI scans reveal how ANO5 muscle disease progresses?
- Can a targeted infusion slow muscle decline in duchenne? a new trial aims to find out.
- Can a massive patient database unlock new treatments for muscular dystrophy?
- Umbilical cord stem cells aim to slow muscle loss in duchenne boys
- Experimental drug aims to preserve arm and lung function in boys with advanced duchenne