New study aims to map rare brain disease in children

NCT ID NCT05825131

First seen May 15, 2026 · Last updated May 15, 2026

Summary

This study follows 30 children and young adults with Sanfilippo syndrome type C, a rare genetic disorder that affects the brain and body. Researchers will collect information from past medical records and future visits to track how the disease progresses over time. The goal is to better understand the condition, which may help design future treatments.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Hospices Civils De Lyon

    RECRUITING

    Bron, 690007539, France

  • The University of Texas Southwestern Medical Center

    RECRUITING

    Dallas, Texas, 75390, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.