New study tracks rare brain disease in children to pave way for future treatments
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This study follows 30 children and young adults with Sanfilippo syndrome type C, a rare genetic disorder that causes severe brain damage. Researchers will measure changes in development and thinking skills over time using standard tests. The goal is to better understand how the d…
Sponsor: Phoenix Nest • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:32 UTC