New RNA drug ORN252 tested in humans for first time

NCT ID NCT07439796

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early-phase study is testing a new experimental drug called ORN252 in 20 healthy adults. ORN252 is a type of RNA therapy wrapped in a fat particle, designed to help the body make a protein that targets certain immune cells. The main goal is to check if it is safe and how the body handles it. This is a first step and does not aim to treat any disease yet.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ORN252 (a lipid nanoparticle containing circular RNA that encodes a CAR protein targeting CD19)

What this could lead to

If safe, this could pave the way for future studies of ORN252 as a potential cancer therapy.

What could go wrong

This is a very early, small phase 1 trial in healthy people, not patients. It only tests safety and how the drug moves through the body, not whether it works against any disease. Side effects are unknown.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Nucleus Network

    RECRUITING

    Herston, Queensland, 4006, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••