New drug could help kids with rare immune disease reach Life-Saving transplant
NCT ID NCT05762640
First seen Apr 25, 2026 · Last updated Apr 29, 2026 · Updated 2 times
Summary
This study tests a drug called ruxolitinib as the first treatment for children with primary hemophagocytic lymphohistiocytosis (HLH), a rare and severe immune disorder. The goal is to see if ruxolitinib, given with steroids, helps children survive long enough to receive a stem cell transplant, which is the only potential long-term control. The study will enroll 20 children up to age 22.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Hopital Necker Enfants malades
RECRUITINGParis, Île-de-France Region, 75015, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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