New drug shows promise for easier breathing during exercise in PAH patients

NCT ID NCT04266197

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tested a single dose of an investigational drug called RT234 in 42 adults with pulmonary arterial hypertension (PAH), a condition that makes it hard to exercise due to high blood pressure in the lungs. The main goals were to see if the drug is safe and if it improves exercise capacity, measured by tests like cycling with breathing analysis and a six-minute walk. Researchers also tracked any side effects and changes in shortness of breath.

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Conditions

The condition(s) this trial relates to.

pulmonary arterial hypertension

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Ascension Seton Medical Center Austin

    Austin, Texas, 78705, United States

  • Augusta University

    Augusta, Georgia, 30912, United States

  • Aurora St. Luke's Medical Center

    Milwaukee, Wisconsin, 53215, United States

  • Baylor Scott and White Institute

    Dallas, Texas, 75246, United States

  • Houston Methodist Hospital

    Houston, Texas, 77030, United States

  • Mayo Clinic

    Rochester, Minnesota, 20010, United States

  • MedStar Heart and Vascular Institute

    Washington D.C., District of Columbia, 20010, United States

  • Medical University of South Carolina

    Charleston, South Carolina, 29425, United States

  • Mount Sinai Hospital

    New York, New York, 10029, United States

  • Norton Health

    Louisville, Kentucky, 40202, United States

  • Ochsner Louisiana State University Health

    Shreveport, Louisiana, 71103, United States

  • The Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

    Torrance, California, 90502, United States

  • The Ohio State University

    Columbus, Ohio, 43210, United States

  • The University of Kansas Medical Center

    Kansas City, Kansas, 66160, United States

  • Tufts University

    Boston, Massachusetts, 02111, United States

  • UC Davis

    Sacramento, California, 95618, United States

  • UCLA

    Los Angeles, California, 90024, United States

  • University Hospital

    Cleveland, Ohio, 44106, United States

  • University of Alabama

    Birmingham, Alabama, 35294, United States

  • University of Arizona

    Tucson, Arizona, 85724, United States

  • University of California San Francisco

    San Francisco, California, 94143, United States

  • University of New Mexico

    Albuquerque, New Mexico, 87131, United States

  • University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, 27514, United States

  • University of Southern California

    Los Angeles, California, 90033, United States

  • Virginia Commonwealth University

    Richmond, Virginia, 23284, United States

  • Washington University

    St Louis, Missouri, 63110, United States