Gene therapy injection aims to restore sight in rare eye disease

NCT ID NCT07303296

First seen Jan 07, 2026 · Last updated May 08, 2026 · Updated 14 times

Summary

This study tests a new drug called GS010, given as an injection into the eye, for people with Leber Hereditary Optic Neuropathy (LHON), a genetic condition that causes rapid vision loss. The goal is to see if the treatment can improve eyesight and boost the activity of energy-producing parts of eye cells. The study involves 14 participants aged 15 and older who have vision loss in both eyes.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

Locations

  • Hopital national des quinze-vingts

    RECRUITING

    Paris, 75012, France

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.