LEBER HEREDITARY OPTIC DISEASE

Clinical trials for LEBER HEREDITARY OPTIC DISEASE explained in plain language.

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Gene therapy injection aims to restore sight in rare blindness

Disease control Recruiting now

This study is testing an experimental gene therapy called GS010 for people with a rare, inherited form of vision loss called ND4 Leber Hereditary Optic Neuropathy (LHON). Researchers are injecting the therapy into both eyes of participants to see if it can improve vision and how …

Matched conditions: LEBER HEREDITARY OPTIC DISEASE

Phase: PHASE2 • Sponsor: GenSight Biologics • Aim: Disease control

Last updated Mar 09, 2026 14:23 UTC

LEBER HEREDITARY OPTIC DISEASE

Get alerted when new LEBER HEREDITARY OPTIC DISEASE trials appear

Gene therapy injection aims to restore sight in rare blindness