Real-World data reveals treatment patterns for kids with SMA
NCT ID NCT07474311
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study analyzed medical records of 213 children with spinal muscular atrophy (SMA) in the Czech and Slovak Republics. Researchers looked at what treatments were used and how the children's motor skills, breathing, and feeding changed over time. The goal was to understand real-world outcomes, not to test a new treatment.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Novartis
Prague, 140 00, Czechia
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