Real-World ravulizumab data: hope for PNH patients in poland

NCT ID NCT06633536

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study follows 64 Polish adults with paroxysmal nocturnal hemoglobinuria (PNH) who are taking ravulizumab as part of their routine care. Researchers will track blood markers like LDH and how many patients need blood transfusions over time. The goal is to see if the drug works as well in everyday life as it did in clinical trials.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ravulizumab

What this could lead to

If successful, this study could confirm that ravulizumab works well in everyday practice for managing PNH, supporting its continued use.

What could go wrong

This is an observational study, not a controlled trial, so results may be less reliable. It only includes 64 patients in Poland, so findings may not apply broadly.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for PAROXYSMAL NOCTURNAL HAEMOGLOBINURIA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Conditions

The condition(s) this trial relates to.

Hemoglobinuria, Paroxysmal paroxysmal nocturnal hemoglobinuria

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Research Site

    Bialystok, Poland

  • Research Site

    Brzozów, Poland

  • Research Site

    Bydgoszcz, Poland

  • Research Site

    Gdansk, Poland

  • Research Site

    Krakow, Poland

  • Research Site

    Lodz, Poland

  • Research Site

    Lublin, Poland

  • Research Site

    Opole, Poland

  • Research Site

    Szczecin, Poland

  • Research Site

    Warsaw, Poland

  • Research Site

    Wałbrzych, Poland