Promising blood cancer combo trial pulled before it even started

NCT ID NCT06284460

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-stage trial aimed to test a combination of two drugs—ASTX727 (already approved for some blood cancers) and ASTX029 (an experimental ERK inhibitor)—in adults with myelodysplastic syndromes (MDS) or related blood cancers that have a mutation in the RAS pathway. The goal was to find a safe dose and see if the combo could control the disease. However, the study was withdrawn before enrolling any participants, so no data were collected.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ASTX727 (decitabine and cedazuridine) and ASTX029 (an ERK inhibitor)

What this could lead to

If this trial had succeeded, it could have pointed toward a new treatment option for people with certain genetic mutations in MDS or MDS/MPN.

What could go wrong

This trial was withdrawn before any participants enrolled, so no results are available. The combination had not been tested in humans, and early-stage cancer trials often fail due to safety or lack of effectiveness.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

atypical chronic myeloid leukemia, BCR-ABL1 negative chronic myelomonocytic leukemia myelodysplastic syndrome myelodysplastic syndrome with excess blasts myelodysplastic/myeloproliferative neoplasm Myeloproliferative Disorders myeloproliferative neoplasm

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • MD Anderson Cancer Cente

    Houston, Texas, 77030, United States