Scientists launch study to track rare GSDs

NCT ID NCT06795152

First seen Jan 11, 2026 · Last updated May 15, 2026 · Updated 22 times

Summary

This study aims to collect and analyze medical information from 200 people with ultra-rare glycogen storage diseases (GSDs), including types 0a, 0b, VII, X, XII, XIII, XV, PRKAG2 syndrome, and Danon disease. Participants must have a confirmed diagnosis. The goal is to better understand how these diseases progress over time, which may help future research. No experimental treatments are involved.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Duke University

    RECRUITING

    Durham, North Carolina, 27710, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.