Engineered probiotic shows promise for PKU in small early trial

NCT ID NCT05948020

First seen Feb 27, 2026 · Last updated May 10, 2026 · Updated 8 times

Summary

This early-phase study tested an engineered probiotic (CBT102-A) in 15 children aged 3–17 with phenylketonuria (PKU), a genetic condition that makes it hard to break down an amino acid called phenylalanine. For 20 days, 10 children received the probiotic and 5 received a placebo. The main goal was to see if the probiotic safely lowers blood phenylalanine levels. Because PKU requires lifelong dietary management, this treatment aims to control the disease rather than cure it.

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Contacts and locations

Locations

  • Children's Hospital of Fudan University

    Shanghai, China

Conditions

Explore the condition pages connected to this study.