Hope for kids with rare gut disease: new drug trial launches
NCT ID NCT07142343
First seen Nov 01, 2025 · Last updated May 10, 2026 · Updated 30 times
Summary
This study tests a drug called pozelimab in 5 children aged 1 to 5 who have CHAPLE disease, a rare inherited condition causing severe stomach and heart problems. The main goal is to see if the drug is safe and what side effects may occur. Researchers will also measure drug levels in the blood and check if it improves protein levels.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for CHAPLE DISEASE are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Marmara University Hospital
RECRUITINGIstanbul, 10 34899, Turkey (Türkiye)
Conditions
Explore the condition pages connected to this study.