New drug duo aims to tame blood disorder when standard meds fail

NCT ID NCT07154745

First seen Nov 01, 2025 · Last updated May 09, 2026 · Updated 28 times

Summary

This study tests two experimental drugs, pozelimab and cemdisiran, together in 35 adults with paroxysmal nocturnal hemoglobinuria (PNH) whose current C5 inhibitor therapy isn't fully controlling red blood cell destruction. The main goal is to see if the combination lowers a key blood marker of hemolysis. Researchers will also monitor side effects and how the body processes the drugs.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • AOU Careggi

    RECRUITING

    Florence, Tuscany, 50134, Italy

  • Ewha Womans University Mokdong Hospital

    RECRUITING

    Seoul, 07985, South Korea

  • Hospital San Pedro de Alcantara

    RECRUITING

    Cáceres, 10003, Spain

  • Hospital Universitario Basurto

    RECRUITING

    Bilbao, Vizcaya, 48013, Spain

  • In-Vivo Sp. z o.o.

    RECRUITING

    Bydgoszcz, Kuyavian-Pomeranian Voivodeship, 85-048, Poland

  • SC Hematology, AOU Città della Salute e della Scienza di Torino

    RECRUITING

    Torino, 10126, Italy

  • Seoul National University Hospital

    RECRUITING

    Seoul, 03080, South Korea

  • Seoul St. Mary's Hospital - The Catholic University of Korea

    RECRUITING

    Seoul, 065791, South Korea

Conditions

Explore the condition pages connected to this study.