Lifeline for severe bleeding disorder: drug access extended
NCT ID NCT06173024
First seen Jun 26, 2026 · Last updated Jun 26, 2026
Summary
This program provides continued compassionate access to recombinant von Willebrand factor (rVWF) for children and adults with severe von Willebrand disease who completed a prior study and are benefiting from treatment. Participants must have no comparable alternative therapy available. The goal is to prevent bleeding complications while no other options exist.
What this could mean
Our plain-language read of the trial. This is informational only — not medical advice or a prediction.
- Active substance
- recombinant von Willebrand factor (rVWF, TAK-577)
- What this could lead to
- If successful, this program ensures continued bleeding control for people with severe von Willebrand disease who have no other treatment options.
- What could go wrong
- This is an access program, not a new trial, so it does not test effectiveness or safety. Only a small number of eligible patients from one prior study can participate.
This is an AI summary of the original study and may miss details. Read our disclaimer.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for SEVERE VON WILLEBRAND DISEASE are added.
By submitting, you agree to our Terms of use
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Email: •••••@•••••
More trials for these conditions
Other studies related to the condition(s) this trial covers.
- New shot aims to tame bleeding disorder in small trial
- New algorithm aims to stop dangerous bleeding in VWD patients
- New hope for kids with rare bleeding disease: study tests rVWF therapy
- Family history questions may improve bleeding disorder detection in kids
- New drug aims to lighten heavy periods for bleeding disorder patients
- UK doctors look back at real-world use of new VWD drug