New study tracks PNH patients in china to understand rare blood disease

NCT ID NCT06154512

First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 24 times

Summary

This study followed 724 people with paroxysmal nocturnal hemoglobinuria (PNH) in China to learn more about the disease and how patients respond to treatments. PNH is a rare blood disorder that can cause red blood cell breakdown, blood clots, and other serious problems. The study observed patients over time to track symptoms, lab results, and outcomes, including those treated with the drug eculizumab. The goal was to fill gaps in knowledge about PNH in Chinese patients and improve future care.

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Contacts and locations

Locations

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    Hefei, Anhui, 230002, China

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    Beijing, Beijing Municipality, 100000, China

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    Beijing, Beijing Municipality, 100044, China

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    Guangzhou, Guangdong, 510080, China

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    Guangzhou, Guangdong, 510180, China

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    Guangzhou, Guangdong, 510515, China

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    Nanning, Guangxi, 530021, China

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    Guiyang, Guizhou, 550004, China

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    Shijiazhuang, Hebei, 050000, China

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    Harbin, Heilongjiang, 150001, China

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    Zhengzhou, Henan, 450003, China

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    Zhengzhou, Henan, 450052, China

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    Zhengzhou, Henan, 463599, China

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    Wuhan, Hubei, 430000, China

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    Wuhan, Hubei, 430030, China

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    Changsha, Hunan, 410005, China

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    Changsha, Hunan, 410008, China

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    Nanjing, Jiangsu, 210029, China

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    Nantong, Jiangsu, 226001, China

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    Xuzhou, Jiangsu, 221002, China

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    Nanchang, Jiangxi, 330006, China

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    Nanchang, Jiangxi, 330008, China

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    Changchun, Jilin, 130021, China

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    Shenyang, Liaoning, 110001, China

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    Jinan, Shandong, 250000, China

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    Qingdao, Shandong, 266000, China

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    Zibo, Shandong, 255090, China

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    Linyi, Shangdong, 276034, China

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    Shanghai, Shanghai Municipality, 200040, China

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    Shanghai, Shanghai Municipality, 200336, China

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    Taiyuan, Shanxi, 030000, China

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    Xi’an, Shanxi, 710061, China

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    Xi’an, Shanxi, 710068, China

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    Chengdu, Sichuan, 610041, China

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    Chengdu, Sichuan, 610072, China

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    Tianjin, Tianjin Municipality, 300020, China

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    Tianjin, Tianjin Municipality, 300052, China

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    Tianjin, Tianjin Municipality, 300190, China

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    Kunming, Yunnan, 650034, China

  • Research Site

    Hangzhou, China

Conditions

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