Massive PNH registry reveals Real-World treatment safety
NCT ID NCT01374360
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study collected health information from over 6,000 people with Paroxysmal Nocturnal Hemoglobinuria (PNH), a rare blood disorder. The goal was to track the safety of two medications, Soliris and Ultomiris, and to understand how PNH changes over time. Participants were followed regardless of whether they took these drugs, helping researchers learn about infections, blood clots, and other serious events.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Contact the PNH Registry at Alexion Pharmaceuticals, Inc. for worldwide locations.
Boston, Massachusetts, 02210, United States
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Other studies related to the condition(s) this trial covers.
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