Landmark study maps rare blood disease in china

NCT ID NCT06154512

Summary

This study aimed to better understand a rare and serious blood disease called Paroxysmal Nocturnal Hemoglobinuria (PNH) in China. Researchers observed 724 patients with PNH to learn about their disease characteristics, symptoms, and how different treatments, including a newer drug called eculizumab, worked in real-world settings. The goal was to gather knowledge to improve future care for people with this condition.

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Contacts and locations

Locations

  • Research Site

    Hefei, Anhui, 230002, China

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    Beijing, Beijing Municipality, 100000, China

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    Beijing, Beijing Municipality, 100044, China

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    Guangzhou, Guangdong, 510080, China

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    Guangzhou, Guangdong, 510180, China

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    Guangzhou, Guangdong, 510515, China

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    Nanning, Guangxi, 530021, China

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    Guiyang, Guizhou, 550004, China

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    Shijiazhuang, Hebei, 050000, China

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    Harbin, Heilongjiang, 150001, China

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    Zhengzhou, Henan, 450003, China

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    Zhengzhou, Henan, 450052, China

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    Zhengzhou, Henan, 463599, China

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    Wuhan, Hubei, 430000, China

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    Wuhan, Hubei, 430030, China

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    Changsha, Hunan, 410005, China

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    Changsha, Hunan, 410008, China

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    Nanjing, Jiangsu, 210029, China

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    Nantong, Jiangsu, 226001, China

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    Xuzhou, Jiangsu, 221002, China

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    Nanchang, Jiangxi, 330006, China

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    Nanchang, Jiangxi, 330008, China

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    Changchun, Jilin, 130021, China

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    Shenyang, Liaoning, 110001, China

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    Jinan, Shandong, 250000, China

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    Qingdao, Shandong, 266000, China

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    Zibo, Shandong, 255090, China

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    Linyi, Shangdong, 276034, China

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    Shanghai, Shanghai Municipality, 200040, China

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    Shanghai, Shanghai Municipality, 200336, China

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    Taiyuan, Shanxi, 030000, China

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    Xi’an, Shanxi, 710061, China

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    Xi’an, Shanxi, 710068, China

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    Chengdu, Sichuan, 610041, China

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    Chengdu, Sichuan, 610072, China

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    Tianjin, Tianjin Municipality, 300020, China

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    Tianjin, Tianjin Municipality, 300052, China

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    Tianjin, Tianjin Municipality, 300190, China

  • Research Site

    Kunming, Yunnan, 650034, China

  • Research Site

    Hangzhou, China

Conditions

Explore the condition pages connected to this study.