Can a liver drug restore color vision? small trial hopes to find out
NCT ID NCT04041232
First seen Sep 30, 2025 · Last updated May 19, 2026 · Updated 36 times
Summary
This early study tests whether an FDA-approved drug called glycerol phenylbutyrate (PBA) can improve vision in people with a rare inherited form of color blindness caused by changes in the ATF6 gene. Only 2 adults with this condition will take the drug three times daily and undergo several eye tests over at least 3 clinic visits. The goal is to see if PBA can reduce stress in the retina and improve color vision and other visual functions.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Columbia University Irving Medical Center
New York, New York, 10032, United States
Conditions
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