New daily shot could replace calcium pills for rare hormone disorder

NCT ID NCT04701203

First seen Jun 27, 2026 · Last updated Jul 08, 2026 · Updated 2 times

Summary

This Phase 3 trial tested a daily injection of TransCon PTH, a synthetic parathyroid hormone, in 84 adults with hypoparathyroidism. The goal was to see if it could help patients maintain normal blood calcium levels while reducing their need for high-dose calcium and vitamin D supplements. Participants were randomly assigned to receive either the active drug or a placebo for 26 weeks, followed by an open-label extension where everyone received the drug.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
TransCon PTH (a daily injection of parathyroid hormone)
What this could lead to
If successful, this could offer a more targeted treatment for hypoparathyroidism, potentially reducing or eliminating the need for high-dose calcium and vitamin D supplements.
What could go wrong
This is a relatively small Phase 3 trial (84 participants), and results may not apply to all patients. The treatment requires daily injections and may have side effects or not work for everyone.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Ascendis Pharma Investigational Site

    San Francisco, California, 94143, United States

  • Ascendis Pharma Investigational Site

    Chicago, Illinois, 60637, United States

  • Ascendis Pharma Investigational Site

    Rochester, Minnesota, 55905, United States

  • Ascendis Pharma Investigational Site

    Reno, Nevada, 89511, United States

  • Ascendis Pharma Investigational Site

    New York, New York, 10032, United States

  • Ascendis Pharma Investigational Site

    Greenville, North Carolina, 27834, United States

  • Ascendis Pharma Investigational Site

    Austin, Texas, 78731, United States

  • Ascendis Pharma Investigational Site

    Fort Worth, Texas, 76132, United States

  • Ascendis Pharma Investigational Site

    Spokane, Washington, 99204, United States

  • Ascendis Pharma Investigational Site

    Halifax, Nova Scotia, B3H 2Y9, Canada

  • Ascendis Pharma Investigational Site

    Oakville, Ontario, L6M 1M1, Canada

  • Ascendis Pharma Investigational Site

    Québec, Quebec, G1V 4G2, Canada

  • Ascendis Pharma Investigational Site

    Copenhagen, Capital Region, 2100, Denmark

  • Ascendis Pharma Investigational Site

    Aarhus, Central Jutland, 8200, Denmark

  • Ascendis Pharma Investigational Site

    Dresden, Saxony, 01307, Germany

  • Ascendis Pharma Investigational Site

    Szeged, Csongrád megye, 6720, Hungary

  • Ascendis Pharma Investigational Site

    Budapest, 1083, Hungary

  • Ascendis Pharma Investigational Site

    Bologna, Emilia-Romagna, 40138, Italy

  • Ascendis Pharma Investigational Site

    Rome, Lazio, 00128, Italy

  • Ascendis Pharma Investigational Site

    Pisa, Piacenza, 56126, Italy

  • Ascendis Pharma Investigational Site

    Oslo, 0176, Norway

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