New PKU drug study aims to unlock a more normal diet and life

NCT ID NCT04404530

Summary

This study is observing adults with PKU who are starting a new, FDA-approved drug called Palynziq. Researchers want to see how this treatment affects what people can eat, their brain function, nutritional status, and overall quality of life over three to five years. The goal is to understand the full impact of this new therapy beyond just lowering blood Phe levels.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Emory University Hospital Georgia Clinical Research Center

    RECRUITING

    Atlanta, Georgia, 30322, United States

  • The Emory Clinic

    RECRUITING

    Atlanta, Georgia, 30322, United States

Conditions

Explore the condition pages connected to this study.