New hope for rare bone marrow cancer patients with dangerous low platelets
NCT ID NCT03165734
First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 24 times
Summary
This study tests a drug called pacritinib against standard treatments in about 400 people with myelofibrosis, a type of bone marrow cancer, who also have very low platelet counts (below 50,000). The goal is to see if pacritinib can shrink the spleen and improve symptoms like belly pain and night sweats. Participants are randomly assigned to receive either pacritinib or a treatment chosen by their doctor.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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ASST Monza - Ospedale San Gerardo
Monza, Italy
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ASST Sette Laghi Hospital
Varese, Italy
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ASST Spedali Civili Brescia, Hematology Unit
Brescia, Italy
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Aktobe Medical Center, Department of Hematology
Aktobe, Kazakhstan
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Alfred Hospital, Malignant Hematology and Stem Cell Transplantation Service
Melbourne, Victoria, Australia
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All India Institute of Medical Sciences
Dehradun, Uttarakhand, India
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American Oncology Partners of Maryland, PA
Bethesda, Maryland, 20817, United States
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Andrzej Mielecki Independent Public Clinical Hospital of Medical University of Silesia in Katowice, Department of Hematology and Bone Marrow Transplantation
Katowice, Poland
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Azienda Ospedaliero-Universitaria Careggi
Florence, Italy
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Barts Health NHS Trust - The Royal London Hospital
London, United Kingdom, E1 2ES, United Kingdom
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Bashkiria State Medical University, Department of Internal Medicine
Ufa, Russia
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Beatson West of Scotland Cancer Centre
Glasgow, United Kingdom, G12 0ZD, United Kingdom
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CHU Hopitaux de Bordeaux - Hôpital Haut-Lévêque
Pessac, 33604, France
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CHU Hôpital Amiens Sud
Amiens, France, 80054, France
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CHU de Nimes - Hopital Universitaire Caremeau
Nîmes, France, 30900, France
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Cancer Institute "Giovanni Paolo II", IRCCS
Bari, Italy
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Cancer and Hematology Centers of Western Michigan
Grand Rapids, Michigan, 49546, United States
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Center for Hematology
Astana, Kazakhstan
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Center for Hematology
Ust-Kamenogorsk, Kazakhstan
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Centre Hospitalier Lyon-Sud
Pierre-Bénite, France
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Cetus Oncology Inc.
Belo Horizonte, Minas Gerais, Brazil
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Cherkasy Regional Oncology Dispensary of Cherkasy Oblast Council, Regional Treatment and Diagnostic Hematology Center, Department of Hematology
Cherkasy, Ukraine
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City Clinical Hospital #4" under Dnipro City Council
Dnipro, Ukraine
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City Clinical Hospital #40
Moscow, Russia
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City Clinical Hospital #7, Hematology Department
Almaty, Kazakhstan
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City Clinical Hospital n.a. V.V. Veresaev of the Moscow City Health
Moscow, Russia
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City Oncological Center
Shymkent, Kazakhstan
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City of Health and Science of Turin
Turin, Italy
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City of Hope
Duarte, California, 91010, United States
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Cleveland Clinic
Cleveland, Ohio, 44106, United States
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Cleveland Clinic Florida
Weston, Florida, 33331, United States
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Clinic UZI 4D, LLC
Pyatigorsk, Russia
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Clinical Center of Serbia, Clinic of Hematology
Belgrade, Serbia
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Clinical Center of Vojvodina, Clinic of Hematology
Novi Sad, Serbia
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Clinical Hospital of the Federal University of Parana (HC - UFPR)
Curitiba, Paraná, Brazil
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Clinics Hospital, Federal University of Goias - (UFG)
Goiânia, Goiás, Brazil
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Coltea Clinical Hospital
Bucharest, Romania
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Columbia University Medical Center
New York, New York, 10017, United States
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Communal Non-profit enterprise "Regional Center of Oncology", Department of Hematology
Kharkiv, Ukraine
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Comprehensive Cancer Centers of Nevada- Twain Office
Las Vegas, Nevada, 89169, United States
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Duke University Hospital
Durham, North Carolina, 27710, United States
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Eastern Regional Health Authority
St. John's, Newfoundland and Labrador, Canada
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Ehime University Hospital
Tōon, Japan
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Fejer County St. Gyorgy University Teaching Hospital, Department of Internal Medicine I
Székesfehérvár, Hungary
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Fortis Memorial Research Institute(FMRI)
Gurgaon, Haryana, India
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Fred Hutchinson Cancer Research Center
Seattle, Washington, 98109, United States
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Frederic Chopin Provincial Teaching Hospital No. 1 in Rzeszow, Department of Hematology,
Rzeszów, Poland
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Fukushima Medical University Hospital
Fukushima, Japan
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Fundeni Clinical Institute
Bucharest, Romania
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Gauhati Medical College and Hospital
Guwahati, Assam, India
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George Washington University-Medical Faculty Associates
Washington D.C., District of Columbia, 20037, United States
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Georgetown University Hospital
Washington D.C., District of Columbia, 20007, United States
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Gloucestershire Royal Hospital
Gloucester, United Kingdom
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Grodno University Hospital
Grodno, Belarus
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Guy's and St Thomas' NHS Foundation Trust - Guy's Hospital
London, United Kingdom
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Hackensack University Medical Center
Hackensack, New Jersey, 07601, United States
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Hadassah Medical Center, Department of Hematology,
Jerusalem, Israel
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Hematology Center
Karaganda, Kazakhstan
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Hospital "Infermi" of Rimini
Rimini, Italy
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Hospital Amaral Carvalho
Jaú, São Paulo, Brazil
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Hospital Clínic de Barcelona
Barcelona, Spain
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Hospital Moinhos de Vento
Porto Alegre, Rio Grande do Sul, Brazil
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Hospital Sao Rafael
Salvador, Estado de Bahia, Brazil
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Hospital Universitario Ramón y Cajal
Madrid, Spain
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Hospital del Mar
Barcelona, Spain
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Humane Clinic / Atena Research Institute
Mossoró, Rio Grande do Norte, Brazil
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Hôpital Saint-Louis
Paris, France
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Icahn School of Medicine at Mount Sinai
New York, New York, 10029, United States
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Imperial College Healthcare NHS Trust - Hammersmith Hospital
London, United Kingdom
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Independent Public Teaching Hospital No.1 in Lublin, Department of Hematooncology, Bone Marrow Transplantation and Chemotherapy
Lublin, Poland
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Institute of Blood Pathology and Transfusion Medicine, Department of Hematology
Lviv, Ukraine
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Institute of Hematology and Transfusion Medicine, Teaching Department of Hematology
Warsaw, Poland
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Integrare Therapeutics
Fortaleza, Ceará, Brazil
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Integrated Oncology Center of Rio Grande do Sul - Mother of God Hospital
Porto Alegre, Rio Grande do Sul, Brazil
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JSC K. Eristavi National Center For Experimental and Clinical Surgery
Tbilisi, Georgia
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Jan Mikulicz Radecki University Hospital in Wroclaw, Department and Clinic of Hematology, Blood Neoplasms and Bone Marrow Transplantation
Wroclaw, Poland
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Jedrzej Sniadecki Specialist Hospital in Nowy Sacz, Department of Hematology
Nowy Sącz, Poland
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Jewish General Hospital; Clinical Research Unit
Montreal, Quebec, Canada
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Jewish Hospital Albert Einstein
São Paulo, São Paulo, Brazil
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Johns Hopkins University
Baltimore, Maryland, 21287, United States
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Juntendo University Hospital
Tokyo, Japan
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Kyiv City Clinical Hospital #9, Hematology Department #1
Kyiv, Ukraine
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Kyiv Regional Oncology Center, Department of Hematology,
Kyiv, Ukraine
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Kyungpook National University Hospital
Daegu, South Korea
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Kyushu University Hospital
Fukuoka, Japan
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LTD M.Zodelava's Hematology Center, Department of Hematology
Tbilisi, Georgia
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LTD S.Khechinashvili University Hospital
Tbilisi, Georgia
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La Conception Hospital
Marseille, France
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Lady Davis Carmel Medical Center, Department of Hematology,
Haifa, Israel
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Limited Liability Company "City Doctor"
Kyiv, Ukraine
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Maggiore Polyclinic Hospital, Fondazione IRCCS Ca' Granda
Milan, Italy
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Malkhaz Katsiashvili Multiprofile Emergency Medicine Center LTD
Tbilisi, Georgia
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Maryland Oncology Hematology, PA- Columbia
Columbia, Maryland, 21044, United States
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Max Super Speciality Hospital Saket (A Unit of Max Healthcare Institute Limited)
Delhi, India
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Mayo Clinic Hospital
Phoenix, Arizona, 85054, United States
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Mays Cancer Center
San Antonio, Texas, 78229, United States
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Meenakshi Mission Hospital And Research Centre (MMHRC)
Madurai, Tamil Nadu, India
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Meir Medical Center, Hematology Institute and Blood Bank
Kfar Saba, Israel
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Memorial Sloan -Kettering Cancer Center
New York, New York, 10065, United States
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Michigan Medicine Hematology Clinic-Rogel Cancer Center
Ann Arbor, Michigan, 48109, United States
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Mie University Hospital
Tsu, Japan
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Minsk Scientific and Practical Center of Surgery, Transplantology and Hematology
Minsk, Belarus
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Morales Meseguer University General Hospital, Department of Hematology and Hemotherapy
Murcia, Spain
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Multiprofile Hospital for Active Treatment "Sveta Marina"
Varna, Bulgaria
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Multiprofile Hospital for Active Treatment - Sofia, part of Military Medical Academy
Sofia, Bulgaria
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Nasz Lekarz Medical Outpatient Clinics Slawomir Jeka
Torun, Poland
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National Research Oncology, Oncohematology Center
Astana, Kazakhstan
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Netaji Subhash Chandra Bose Cancer Research Institute
Kolkata, West Bengal, India
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Nicolaus Copernicus Provincial Multispecialty Oncology and Traumatology Center in Lodz
Lodz, Poland
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Nippon Medical School Hospital
Tokyo, Japan
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Nirmal Hospital Pvt Ltd
Surat, Gujarat, India
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Northwestern Memorial Hospital
Chicago, Illinois, 60611, United States
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Nova Scotia Health Authority, Centre for Clinical Research
Halifax, Nova Scotia, Canada
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Ochsner Medical Center
New Orleans, Louisiana, 70121, United States
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Onco Card Srl
Brasov, Romania
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Oregon Health and Science University
Portland, Oregon, 97239-3098, United States
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Oxford University Hospitals NHS Trust - Churchill Hospital
Oxford, United Kingdom
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Poltava M.V. Sklifosovskyi Regional Clinical Hospital under Poltava Regional Council, Department of Hematology
Poltava, Ukraine
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Polyclinic S. Orsola-Malpighi
Bologna, Italy
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Polyclinic San Matteo, IRCCS
Pavia, Italy
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Postgraduate Institute of Medical Education and Research (PGIMER)
Chandigarh, Chandigarh, India
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Pratia Oncology Katowice
Katowice, Poland
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Princess Margaret Cancer Centre
Toronto, Ontario, Canada
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Prof. Dr. Ion Chiricuta" Institute of Oncology
Cluj-Napoca, Romania
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Providence Hematology - Vancouver
Vancouver, British Columbia, Canada
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Pusan National University Hospital
Busan, South Korea
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Rabin Medical Center, Clinic for Myeloproliferative Disorders
Petah Tikva, Israel
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Regional Cancer Care Associates LLC - CCBD Division
Bethesda, Maryland, 20817, United States
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Republican Research Center for Radiation Medicine and Human Ecology
Homyel, Belarus
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Research Institute of Hematology and Transfusiology
Saint Petersburg, Russia
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Rocky Mountain Cancer Centers (US Oncology/McKesson)
Boulder, Colorado, 80303, United States
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Royal Hallamshire Hospital, Department of Hematology
Sheffield, South Yorkshire, United Kingdom
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Rush University Medical Center
Chicago, Illinois, 60612, United States
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S.M. Kirov Military Medical Academy, Department and Clinic for Intermediate-Level Training in Internal Medicine, Hematology Division
Saint Petersburg, Russia
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S.P. Botkin City Clinical Hospital
Moscow, Russia
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Sahyadri Super Speciality Hospital
Pune, Maharashtra, India
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Saint Agnes Hospital
Baltimore, Maryland, 21229, United States
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Saint Lucas Hospital of Copacabana
Rio de Janeiro, Rio de Janeiro, Brazil
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Samaritano Hospital
São Paulo, São Paulo, Brazil
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Samsung Medical Center
Seoul, South Korea
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Santa Catarina Health Research and Education Center (CEPEN)
Florianópolis, Santa Catarina, Brazil
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Santa Maria della Misericordia University Hospital of Udine
Udine, Italy
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Sao Paulo University Clinical Hospital
São Paulo, São Paulo, Brazil
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Scientific Institute of Romagna for the Study and Treatment of Cancer (IRST), IRCCS
Forlì, Italy
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Semmelweis University SE ÁOK I. sz. Belgyógyászati Klinika
Budapest, Hungary
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Seoul National University Hospital
Seoul, South Korea
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Severance Hospital
Seoul, South Korea, 3722, South Korea
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Shri Ram Cancer Centre, Mahatma Gandhi Medical College & Hospital
Jaipur, Rajasthan, India
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Somogy Megyei Kaposi Mór Oktató Kórház
Kaposvár, Hungary
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Specialized Hospital for Active Treatment of Hematological Diseases
Sofia, Bulgaria
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St. John's Medical College Hospital
Bengaluru, India
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State University of Campinas (UNICAMP) - Hemocenter
Campinas, São Paulo, Brazil
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Szabolcs-Szatmar-Bereg County Hospitals and University Teaching Hospital, Department of Hematology
Nyíregyháza, Hungary
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Tata Medical Center
Kolkata, West Bengal, India
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Tbilisi State Medical University and Ingorokva High Medical Technology University Clinic LLC
Tbilisi, Georgia
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Texas Oncology- San Antonio
San Antonio, Texas, 78240, United States
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The Catholic University of Korea, St. Mary's Hospital
Seoul, South Korea
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The James Cancer Hospital and Solove Research Institute
Columbus, Ohio, 43210, United States
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The Perth Blood Institute
Perth, Western Australia, Australia
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The Sarah Cannon Research Institute-Tennessee Oncology
Nashville, Tennessee, 37203, United States
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The Tel Aviv Sourasky Medical Center, Department of Internal Medicine
Tel Aviv, Israel
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The University of Chicago Medical Center
Chicago, Illinois, 60637, United States
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The University of Texas MD Anderson Cancer Center
Houston, Texas, 77030, United States
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Tohoku University Hospital
Miyagi, Japan
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Tokyo Medical University Hospital
Tokyo, Japan
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Tom Baker Cancer Center, Internal Medicine/Hematology
Calgary, Alberta, Canada
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UCLA David Geffen School of Medicine
Los Angeles, California, 90095, United States
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UPMC Hillman Cancer Center
Pittsburgh, Pennsylvania, 15232, United States
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USC Norris Comprehensive Cancer Center
Los Angeles, California, 90033, United States
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Umberto I Polyclinic of Rome
Rome, Italy
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United Hospitals Villa Sofia Cervello
Palermo, Italy
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University Clinical Center in Gdansk
Gdansk, Poland
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University Clinical Center of Sarajevo
Sarajevo, Bosnia and Herzegovina
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University Clinical Centre of the Republic of Srpska
Banja Luka, Bosnia and Herzegovina
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University Clinical Hospital of Salamanca, Department of Hematology
Salamanca, Spain
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University Clinical Hospital of Valencia, Department of Hematology and Medical Oncology
Valencia, Spain
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University Hospital "Federico II"
Naples, Italy
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University Hospital "Maggiore della Carita" of Novara
Novara, Italy
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University Hospital 12 de Octubre, Department of Hematology
Madrid, Spain
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University Hospital Brno
Brno, Czechia
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University Hospital Center of Poitiers
Poitiers, France
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University Hospital Kralovske Vinohrady, Clinic of Internal Hematology
Prague, Czechia
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University Hospital Olomouc
Olomouc, Czechia
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University Hospital Plzen
Pilsen, Czechia
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University Hospital Vall d'Hebron
Barcelona, Spain
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University Hospital Virgen del Rocio (HUVR)
Seville, Spain
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University Hospital in Krakow
Krakow, Poland
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University Multiprofile Hospital for Active Treatment "Dr. Georgi Stranski"
Pleven, Bulgaria
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University Multiprofile Hospital for Active Treatment "Sveti Georgi", Plovdiv
Plovdiv, Bulgaria
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University Polyclinic Foundation "Agostino Gemelli"
Rome, Italy
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University Teaching Hospital in Bialystok
Bialystok, Poland
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University of Alabama at Birmingham, (UAB) Hospital, Comprehensive Cancer Center
Birmingham, Alabama, 35294, United States
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University of Alberta
Edmonton, Alberta, Canada
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University of Colorado Cancer Center
Aurora, Colorado, 80045, United States
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University of Debrecen Clinical Center (Debreceni Egyetem Klinikai Központ)
Debrecen, Hungary
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University of Kansas Cancer Center and Medical Pavilion
Westwood, Kansas, 66205, United States
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University of Miyazaki Hospital
Miyazaki, Japan
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University of Rochester
Rochester, New York, 14642, United States
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University of Utah - Huntsman Cancer Institute
Salt Lake City, Utah, 84112, United States
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University of Yamanashi Hospital
Chūō, Japan
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V.A. Almazov North-West Federal Medical Research Center, Institute of Oncology and Hematology, Scientific Department of Clinical Oncology
Saint Petersburg, Russia
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Volgograd Regional Clinical Oncology Center
Volgograd, Russia
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Washington University School of Medicine-Siteman Cancer Center
St Louis, Missouri, 63110, United States
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Weill Cornell Medical College
New York, New York, 10021, United States
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Westmead Hospital
Sydney, New South Wales, Australia
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Yale School of Medicine
New Haven, Connecticut, 06510, United States
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Yashoda Hospitals
Hyderabad, Telangana, India
Conditions
Explore the condition pages connected to this study.