New drug shows promise for rare energy disorder

NCT ID NCT05972954

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study tested a new drug called OMT-28 in 28 people with primary mitochondrial disease, a condition that affects how cells produce energy. Participants took the drug once daily for 6 months, and researchers measured safety, blood markers of inflammation, and symptoms like fatigue. The goal was to see if OMT-28 is safe and could improve disease signs.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

OMT-28 (a drug taken once daily)

What this could lead to

If it works, this could point toward a treatment that reduces inflammation and improves energy levels in people with mitochondrial disease.

What could go wrong

This is a small, early-phase trial with only 28 participants, so results may not apply to everyone. The drug may not show clear benefits or could cause side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

cardiomyopathy Deafness lactic acidosis maternally-inherited diabetes and deafness MELAS syndrome MERRF syndrome mitochondrial disease Mitochondrial encephalopathy muscle tissue disorder syndromic disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

More trials for these conditions

Other studies related to the condition(s) this trial covers.

Contacts and locations

Locations

  • Azienda Ospedaliero Universitaria Pisana, P.O. Santa Chiara, U.O. Neurologia, Edificio 13, Via Roma 67

    Pisa, 56126, Italy

  • Friedrich-Baur-Institut an der Neurologischen Klinik und Poliklinik, Klinikum der Universität München, Ludwig-Maximilians-Universität (LMU Klinikum), Ziemssenstr. 1a

    Munich, 80336, Germany

  • IRCCS Institute of Neurological Science of Bologna, University of Bologna, Department of Biomedical and Neuromotor Science (DIBINEM), Ospedale Bellaria Via Altura, 3

    Bologna, 40139, Italy

  • IRCCS Istituto Neurologico Carlo Besta, SC Servizio Di Medicina Di Laboratorio - Genetica Medica E Neurogenetica, Via Celoria 11

    Milan, 20133, Italy

  • Medizinisch Fakultät der Martin-Luther-Universität Halle-Wittenberg Universitätsklinik und Poliklinik für Neurologie Universitätsklinikum , Ernst-Grube-Str. 40

    Halle, 06120, Germany

  • Radboud University Nijmegen Medical Centre

    Nijmegen, Gelderland, 6500 HB, Netherlands

  • U.O.C. di Neurologia e Malattie Neuromuscolari

    Messina, 98125, Italy

  • UOC di neurofisiopatologia

    Roma, 8-00168, Italy

  • Universitätsklinikum Bonn, Sektion Neuromuskuläre Erkrankungen, Klinik und Poliklinik für Neurologie, Venusberg-Campus 1, Gebäude 80, NPP

    Bonn, 53127, Germany