Children's FA drug trial opens: could omaveloxolone help younger patients?

NCT ID NCT06054893

First seen Nov 01, 2025 · Last updated May 02, 2026 · Updated 25 times

Summary

This study tests an approved FA drug (omaveloxolone) in 35 children aged 2 to 15 to see how their bodies process it and whether it is safe. The drug is already available for patients 16 and older. Researchers will monitor side effects, growth, and heart health over up to 240 weeks.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact

    Contact Phone: •••-•••-••••

Conditions

Explore the condition pages connected to this study.