New drug duo aims to tame High-Risk MDS

NCT ID NCT03564873

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests two drugs—omacetaxine and azacitidine—given together to people with untreated high-grade myelodysplastic syndromes (MDS), a serious bone marrow condition. The first part finds the safest dose of omacetaxine, and the second part checks how many patients achieve remission. About 28 adults will take part, receiving the drugs for 7 days each month.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

omacetaxine and azacitidine

What this could lead to

If successful, this combination could offer a new treatment option for people with high-grade myelodysplastic syndromes, potentially improving remission rates.

What could go wrong

This is a small, early-phase trial (Phase 1/2) with only 28 participants, so results may not apply broadly. The drugs can cause side effects like low blood counts and infection risk.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

chronic myelomonocytic leukemia myelodysplastic syndrome myelodysplastic syndrome with excess blasts

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Universtiy of Colorado Denver

    Aurora, Colorado, 80045, United States