One-Shot gene therapy aims to halt rare, blinding eye disease in young people
NCT ID NCT05956626
First seen Nov 01, 2025 · Last updated Apr 06, 2026 · Updated 21 times
Summary
This study is testing a one-time gene therapy called OCU410ST for Stargardt disease, a genetic condition that causes progressive vision loss in children and young adults. The therapy is delivered via a single injection into the eye and aims to slow or stop the disease by restoring healthy cell function. The trial will enroll 51 participants, with about two-thirds receiving the treatment and the rest being followed as an untreated comparison group.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Locations
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Advanced Research, LLC
RECRUITINGPompano Beach, Florida, 33064, United States
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Associated Retina Consultants
RECRUITINGPhoenix, Arizona, 85020, United States
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Bascom Palmer Eye Institute
RECRUITINGMiami, Florida, 33136, United States
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Boston Children's Hospital
RECRUITINGBoston, Massachusetts, 02115, United States
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Duke Eye Center
RECRUITINGDurham, North Carolina, 27710, United States
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Erie Retina Research, LLC
RECRUITINGErie, Pennsylvania, 16505, United States
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Mississippi Retina Associates
RECRUITINGJackson, Mississippi, 39202, United States
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Retina Consultants of Texas
RECRUITINGBellaire, Texas, 77401, United States
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Retina Foundation of the Southwest
RECRUITINGDallas, Texas, 75231, United States
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Retina Partners Midwest, P.C.
RECRUITINGCarmel, Indiana, 46032, United States
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Retinal Consultants Medical Group
NOT_YET_RECRUITINGSacramento, California, 95825, United States
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Contact Phone: •••-•••-•••• Email: •••••@•••••
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The Retina Institute
RECRUITINGSt Louis, Missouri, 63128, United States
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Valley Retina Institute
RECRUITINGMcAllen, Texas, 78503, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Vitreo Retinal Associates, P.A.
RECRUITINGGainesville, Florida, 32607, United States
Contact Email: •••••@•••••
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Conditions
Explore the condition pages connected to this study.