New pill shows promise for rare blood disorder in Long-Term trial

NCT ID NCT07177872

First seen Nov 01, 2025 · Last updated May 08, 2026 · Updated 24 times

Summary

This study looks at the long-term safety and effectiveness of NTQ5082 capsules for people with paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disease. About 78 adults who have already benefited from NTQ5082 or are on standard treatment will take the drug for up to several years. The goal is to see if NTQ5082 can keep red blood cell levels healthy without transfusions.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences ,

    Tianjin, Tianjin Municipality, 300020, China

    Contact

    Contact

Conditions

Explore the condition pages connected to this study.