New pill could help PNH patients avoid transfusions

NCT ID NCT07177859

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 24 times

Summary

This study tests a new oral medication, NTQ5082, for people with paroxysmal nocturnal hemoglobinuria (PNH), a rare blood disorder that destroys red blood cells. The trial will include about 78 adults who have not received prior complement inhibitor therapy. The main goal is to see if NTQ5082 can raise hemoglobin levels to normal without needing blood transfusions.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences

    Tianjin, Tianjin Municipality, 300020, China

    Contact

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Conditions

Explore the condition pages connected to this study.