Immunotherapy combo shows promise for rare childhood tumors

NCT ID NCT04416568

First seen Jun 24, 2026 · Last updated Jul 01, 2026 · Updated 2 times

Summary

This phase 2 trial is testing two immunotherapy drugs, nivolumab and ipilimumab, in children and young adults with rare INI1-negative cancers that have come back or not responded to treatment. The study aims to see if the combination can shrink tumors or slow disease progression. About 45 participants with specific tumor types are being enrolled.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

nivolumab and ipilimumab (immunotherapy drugs)

What this could lead to

If this works, it could offer a new treatment option for children and young adults with rare INI1-negative cancers that have not responded to standard therapies.

What could go wrong

This is a small, early-phase study (45 participants) with no control group, so results may not apply broadly. Immunotherapy can cause serious side effects like inflammation of organs.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

atypical teratoid rhabdoid tumor chordoma epithelioid sarcoma poorly differentiated chordoma rhabdoid tumor rhabdoid tumor of the kidney sarcoma SMARCA4-deficient sarcoma of thorax

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Boston Children's Hospital

    Boston, Massachusetts, 02115, United States

  • Children's Healthcare of Atlanta-Egleston

    Atlanta, Georgia, 30322, United States

  • Children's Healthcare of Atlanta-Scottish Rite

    Atlanta, Georgia, 30342, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

  • Texas Children's Hospital

    Houston, Texas, 77030, United States

  • UCSF Benioff Children's Hospital

    San Francisco, California, 94158, United States