HT-1 drug study in china withdrawn before starting

NCT ID NCT06227429

First seen Jun 27, 2026 ยท Last updated Jun 27, 2026

Summary

This study was designed to observe how patients with hereditary tyrosinemia type 1 (HT-1) in China respond to nitisinone treatment in everyday medical practice. It planned to track serious health events like liver problems or death. However, the study was withdrawn before enrolling any participants, so no data were collected.

What this could mean

Our plain-language read of the trial. This is informational only โ€” not medical advice or a prediction.

Active substance
nitisinone (Orfadin)

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Swedish Orphan Biovitrum Research Site

    Beijing, China

  • Swedish Orphan Biovitrum Research Site

    Chongqing, China

  • Swedish Orphan Biovitrum Research Site

    Hefei, China

  • Swedish Orphan Biovitrum Research Site

    Wuhan, China