Implanted port offers hope for SMA patients who Can't get standard spinal injections

NCT ID NCT05866419

Summary

This study is testing a small, implanted port and catheter system designed to deliver medication directly to the spinal fluid for people with spinal muscular atrophy (SMA) who cannot receive standard lumbar puncture injections. The device is intended for patients aged 3 and older who have difficulty with repeated spinal taps due to spinal deformities or other health risks. Researchers will follow 90 participants for 12 months to see if the implanted system safely and effectively delivers the SMA drug nusinersen.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Barrow Neurological Institute

    RECRUITING

    Phoenix, Arizona, 85013, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Email: •••••@•••••

  • Centro Clinico Nemo

    WITHDRAWN

    Milan, 20162, Italy

  • Children's Hospital Orange County

    RECRUITING

    Orange, California, 92868, United States

    Contact Email: •••••@•••••

  • Children's Hospital Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Email: •••••@•••••

  • Childrens Hospital of the King's Daughters

    RECRUITING

    Norfolk, Virginia, 23510, United States

    Contact Email: •••••@•••••

  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital

    RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Helen DeVos Children's Hospital

    RECRUITING

    Grand Rapids, Michigan, 49503, United States

    Contact Email: •••••@•••••

  • Hospital Universitario La Paz

    RECRUITING

    Madrid, Spain

    Contact Email: •••••@•••••

  • Hospital Universitario y Politecnico la Fe de Valencia

    RECRUITING

    Valencia, 46026, Spain

    Contact Email: •••••@•••••

  • Lurie Childrens Hospital

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact Email: •••••@•••••

    Contact

  • Penn State Milton S. Hershey Medical Center

    RECRUITING

    Hershey, Pennsylvania, 17033, United States

    Contact Email: •••••@•••••

  • Rady Children's Hospital

    RECRUITING

    San Diego, California, 92037, United States

    Contact Email: •••••@•••••

  • Research Institute of Polish Mother's Memorial Hospital

    RECRUITING

    Lodz, Poland

    Contact Email: •••••@•••••

  • Sheffield Teaching Hospitals NHS Foundation Trust

    RECRUITING

    Sheffield, United Kingdom

    Contact Email: •••••@•••••

  • Specialised Hospital Ludwika Rydygiera

    RECRUITING

    Krakow, Poland

    Contact Email: •••••@•••••

  • Stanford Medical Center

    RECRUITING

    Palo Alto, California, 94301, United States

    Contact Email: •••••@•••••

  • Texas Children's Hospital

    RECRUITING

    Houston, Texas, 77030, United States

    Contact Email: •••••@•••••

  • UH Rainbow Babies and Children's Hospital

    RECRUITING

    Cleveland, Ohio, 44106, United States

    Contact Email: •••••@•••••

  • University of Virginia

    RECRUITING

    Charlottesville, Virginia, 22903, United States

    Contact Email: •••••@•••••

    Contact

  • Universitätsklinikum Essen

    RECRUITING

    Essen, Germany

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.