Scientists track rare muscle disease to pave way for future treatments
NCT ID NCT07201636
Summary
This study aims to better understand how nemaline myopathy, a rare genetic muscle disorder, progresses over time. Researchers will follow 10 patients of any age for three years, collecting information during their regular hospital visits about movement, breathing, and quality of life. The goal is to gather essential data that will help design future treatment trials for this condition.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle
Liège, 4000, Belgium
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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