New hope for kids with severe bleeding disorder
NCT ID NCT02137850
Summary
This study tested a medication called N8-GP in young children with severe hemophilia A who had never received treatment. The goal was to see if it was safe and effective at preventing bleeding episodes and stopping bleeds when they occurred. Researchers followed 124 boys under age 6 to monitor for side effects and measure how well the treatment controlled their condition.
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Contacts and locations
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Locations
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'Ippokrateio' General Hospital of Thessaloniki
Thessaloniki, 54642, Greece
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,,Louis Ţurcanu'' Emergency Hospital for Children
Timișoara, Timiș County, 300011, Romania
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1st Paediatric Department, Fundeni Clinical Institute
Bucharest, 022328, Romania
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A.O.U. Città della Salute e della Scienza di Torino-Ospedale
Torino, 10126, Italy
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Aghia Sophia Childrens' Hospital
Athens, GR-11527, Greece
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Ap-Hp-Hopital Necker-1
Paris, 75015, France
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Arizona H&T Phoenix Child Hosp
Phoenix, Arizona, 85016-7710, United States
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Beni Messous Hospital Issaad Hassani
Algiers, 16000, Algeria
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CHU Estaing
Clermont-Ferrand, 63003, France
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Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu
Nantes, 44093, France
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Centro Hospitalar Lisboa Norte-HSM
Lisbon, 1649-035, Portugal
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Centro Medico Nacional SXXI-Hospital de Pediatria, IMSS
Mexico City, México, D.F., 06720, Mexico
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Changhua Christian Hospital_Hematology Dept.
Changhua, 500, Taiwan
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Children's Hosp Of Orange
Orange, California, 92868-3835, United States
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Children's Hosp-New Orleans
New Orleans, Louisiana, 70118-5720, United States
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Children's Hospital Los Angeles - Endocrinology
Los Angeles, California, 90027, United States
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Children's Hosptl Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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Children's Hsptl Of The Kings
Norfolk, Virginia, 23507, United States
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China Medical University Children's Hospital
Taichung, 40447, Taiwan
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Coagulation Research Center
Duisburg, 47051, Germany
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Dayton Children Hemostati Ctr
Dayton, Ohio, 45404, United States
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Dipartimento di Ematologia Univ. Firenze
Florence, 50134, Italy
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Emergency County Hospital Constanta
Constanța, 900591, Romania
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Emory University_Atlanta_1
Atlanta, Georgia, 30322, United States
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HZRM Haemophilie-Zentrum Rhein Main GmbH
Frankfurt am Main, 60596, Germany
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Hamltn Hth Sci/McMstr Child Hosp
Hamilton, Ontario, L8N 3Z5, Canada
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Harbor-UCLA Medical Center
Torrance, California, 90502-2004, United States
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Health Science Centre
St. John's, Newfoundland and Labrador, A1B 3V6, Canada
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Hemostasis and Thrombosis Center of Nevada
Las Vegas, Nevada, 89113, United States
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Hospices Civils de Lyon- Hopital Louis Pradel-1
Bron, 69500, France
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Hospital Pulau Pinang_Georgetown, Penang
George Town, Pulau Pinang, 10450, Malaysia
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Hospital Sant Joan de Déu
Esplugues Llobregat, 08950, Spain
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Hospital Teresa Herrera Materno Infantil . E.O.X.I. A Coruña
A Coruña, 15006, Spain
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Hospital Universitario Dr. José Eleuterio González_Monterrey
Monterrey, Nuevo León, 64460, Mexico
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Wanita dan Kanak-Kanak Kuala Lumpur
Kuala Lumpur, 50300, Malaysia
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Hospital de Pediatría S.A.M.I.C. "Prof. Dr. Juan P. Garrahan
CABA, C1245AAM, Argentina
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Hyogo prefectural kobe children's hospital
Hyōgo, 654-0047, Japan
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IRCCS Meyer Firenze
Florence, 50139, Italy
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Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery
Lviv, 79044, Ukraine
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Kaohsiung Medical University Chung-Ho Memorial Hospital_Dept of Pediatrics
Kaohsiung City, 807, Taiwan
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Klinikum Klagenfurt am Wörthersee (LKH Klagenfurt)
Klagenfurt, 9020, Austria
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LKH Salzburg- Univ. Klinik f. Kinder- und Jugendheilkunde
Salzburg, 5020, Austria
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LKH St. Poelten, Kinder-und Jugendheilkunde
Sankt Pölten, 3100, Austria
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Lady Cilento Children's Hospital
South Brisbane, Queensland, 4101, Australia
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Landes-Frauen und Kinderklinik Linz
Linz, 4020, Austria
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Maharaj Nakorn Chiang Mai Hospital _Pediatric Hematology and Oncology
Chiang Mai, 50200, Thailand
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Master centre for France
Paris La Défense, 92936, France
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Med. Univ. Graz -Klinische Abteilung f. Allgemeine Pädiatrie
Graz, 8036, Austria
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Medical College Of Georgia
Augusta, Georgia, 30912, United States
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Medical University Of SC
Charleston, South Carolina, 29425, United States
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Miller Children's Hospital Long Beach
Long Beach, California, 90806, United States
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Nagoya University Hospital_Blood Transfusion
Aichi, 466-8560, Japan
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National Blood Centre
Kuala Lumpur, 50400, Malaysia
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National Center for Child Health and Development_Hematology
Tokyo, 157-8535, Japan
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National Taiwan University Children's Hospital
Taipei, 100, Taiwan
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Nemours Child Orlando Hem/Onc
Orlando, Florida, United States
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Nemours Chld Clnc Jacksonville
Jacksonville, Florida, 32207, United States
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North Shore Long Island Jewish Medical Center
New Hyde Park, New York, 11042, United States
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Novant Hlth Vasc Ins Charlotte
Charlotte, North Carolina, 28204, United States
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Oregon Health & Science University_Portland_5
Portland, Oregon, 97239, United States
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Pediatric Hemophilia Program University
San Juan, 00935, Puerto Rico
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Ramathibodi Hospital_Paediatrics
Bangkok, 10400, Thailand
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Royal Children's Hospital
Parkville, Victoria, 3052, Australia
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Rush University Med. Cntr
Chicago, Illinois, 60612, United States
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Rutgers-Robert Wood Johnson Medical School
New Brunswick, New Jersey, 08901, United States
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SI Institute of Urgent and Recovery Surgery - Haematology
Donetsk, 83045, Ukraine
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Saitama Children's Med Centre_Hematology-Oncology
Saitama, 330-8777, Japan
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Sanatorio Mayo Privado S.A
Córdoba, X5000FAL, Argentina
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Shands Hospital at the University of Florida
Gainesville, Florida, 32610, United States
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Sheba MC - The Israeli National Hemophilia Center
Tel Litwinsky, 52621, Israel
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Shizuoka Children's Hospital, Hematology-Oncology
Shizuoka, 420-8660, Japan
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St Christopher Hosp for Child
Philadelphia, Pennsylvania, 19134, United States
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St Joseph's Hospital Foundation
Tampa, Florida, 33607, United States
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St. Luke's Mountain States Tumor Institute
Boise, Idaho, 83712, United States
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Sunpasitthiprasong Hospital_Pediatrics Department
Ubon Ratchathani, Mueang Distirct,, 34000, Thailand
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The Brooklyn Hsptl Center
Brooklyn, New York, 11201-5425, United States
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Torrence Hemby Ped Hem/Onc Ctr
Charlotte, North Carolina, 28203, United States
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Tulane University School of Medicine
New Orleans, Louisiana, 70112, United States
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ULS São João, E.P.E.
Porto, 4200-319, Portugal
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UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics
Plovdiv, 4002, Bulgaria
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Univ Hosp Cleveland Med Ctr
Cleveland, Ohio, 44106, United States
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Univ Oklahoma Sci Ctr OK City
Oklahoma City, Oklahoma, 73104, United States
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Univ of NE Med Center_Omaha
Omaha, Nebraska, 68198-6828, United States
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Univ of Utah Primary Children's Hospital
Salt Lake City, Utah, 84113, United States
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Univ.HP, Kyoto Pref Univ of Medicine, Dept. of Pediatrics
Kyoto, 602-8566, Japan
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University Children's Hospital Tirsova
Belgrade, 11000, Serbia
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University Hospital Saadna Abdenour of Setif
Sétif, 19000, Algeria
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University Of Iowa
Iowa City, Iowa, 52242, United States
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University Of Virginia Hospitl
Charlottesville, Virginia, 22908, United States
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Universitätsklinik Kinder-Jugendheilkunde Innsbruck
Innsbruck, 6020, Austria
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Universitätsklinik für Kinder- und Jugendheilkunde
Vienna, A 1090, Austria
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Universitätsklinikum des Saarlandes - Pädiatrische Onkologie und Hämatologie
Homburg/Saar, 66424, Germany
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Vanderbilt Hemostasis Thrombosis Clinic
Nashville, Tennessee, 37232, United States
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Werlhof-Institut
Hanover, 30159, Germany
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Werlhof-Institut
Hanover, Germany
Conditions
Explore the condition pages connected to this study.