New drug combo aims to tame debilitating muscle disease
NCT ID NCT05070858
Summary
This study is testing two new drugs, pozelimab and cemdisiran, to see if they can better control the muscle weakness and fatigue caused by generalized myasthenia gravis (gMG). It will involve about 288 adults with gMG to compare the effectiveness and safety of using the drugs together versus using cemdisiran alone. The main goal is to see if the treatments can help patients perform daily activities more easily.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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AZ Sint-Lucas
Ghent, Oost-Vlaanderen, 9000, Belgium
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Aalborg Universitetshospital
Aalborg, North Denmark, 09000, Denmark
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Aarhus University Hospital
Aarhus N, 8200, Denmark
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All India Institute of Medical Sciences New Delhi
New Delhi, National Capital Territory of Delhi, 110029, India
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Amrita Institute of Medical Sciences and Research Centre (AIMS)
Kochi, Kerala, 682041, India
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Apex Hospital
Jaipur, Rajasthan, 302017, India
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Aqualane Clinical Research
Naples, Florida, 34105, United States
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Azienda Ospedaliera Papa Giovanni XXIII
Bergamo, 24127, Italy
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Azienda Ospedaliera Sant'andrea
Rome, Lazio, 00189, Italy
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Azienda Ospedaliero Universitaria Pisana
Pisa, Tuscany, 56126, Italy
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Bangalore Medical College and Research Institute (BMCRI) - Victoria Hospital
Bangalore, 560002, India
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CHU Bicetre
Le Kremlin-Bicêtre, 94275, France
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Centre Hospitalier Regional Universitaire (CHRU) de Nancy
Nancy, 54035, France
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Centre Hospitalier Universitaire de Nice
Nice, Alpes Maritimes, 6002, France
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Centrum Neurologii Klinicznej, Krakowska Akademia Neurologii
Krakow, Lesser Poland Voivodeship, 31-505, Poland
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Chang Gung Memorial Foundation Kaohsiung Branch
Kaohsiung City, 833, Taiwan
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Chang Gung Memorial Hospital at Linkou
Taoyuan District, 333, Taiwan
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Charite - Universitatsmedizin Berlin
Berlin, 10117, Germany
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Chiba University Hospital
Chiba, 260-8677, Japan
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China Medical University
Taichung, 40447, Taiwan
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Christian Medical College & Hospital
Ludhiana, Punjab, 141008, India
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City Neuro Centre, Hyderabad
Hyderabad, Telangana, 500034, India
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Clinical Research Center Spolka z Ograniczona Odpowiedzialnoscia Medic-R Sp.k
Poznan, Greater Poland Voivodeship, 61-731, Poland
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Colorado Springs Neurological Associates
Colorado Springs, Colorado, 80907-5307, United States
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Dayton Center for Neurological Disorders
Centerville, Ohio, 45459, United States
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Deenanath Mangeshkar Hospital and Research Centre
Pune, Maharashtra, 411004, India
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Diverse Clinical Research
Miami, Florida, 33175, United States
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Dokuz Eylul University Medical Faculty
Izmir, 35340, Turkey (Türkiye)
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Faculdade de Medicina Do ABC
Santo André, São Paulo, 09060-870, Brazil
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Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta
Milan, Lombardy, 20133, Italy
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Friedrich Baur Institute
München, Bavaria, 80336, Germany
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Fujian Medical University Union Hospital
Fuzhou, Fujian, 350001, China
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Gdanski Uniwersytet Medyczny
Gdansk, Pomeranian Voivodeship, 80-952, Poland
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Government General Hospital, Guntur
Guntur, Andhra Pradesh, 522001, India
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Guangdong Hospital of Traditional Chinese Medicine
Guangdong, Guangdong, 510120, China
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Hainan General Hospital
Haikou, Hainan, 570311, China
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Hiroshima City Hiroshima Citiz
Hiroshima, 730-8518, Japan
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HonorHealth Neurology 2018
Scottsdale, Arizona, 85251, United States
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Hopital de la Pitie Salpetriere
Paris, 75013, France
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Hospital Universitari i Politecnic La Fe
Valencia, 46026, Spain
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Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo
São Paulo, 05403-010, Brazil
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Hospital de la Santa Creu i Sant Pau
Barcelona, 08041, Spain
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Huashan Hospital Fudan University
Shanghai, Shanghai Municipality, 201107, China
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IMV Pesquisa Neurologica
Porto Alegre, Rio Grande do Sul, 90110-000, Brazil
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Institute of Neurosciences
Surat, Gujarat, 395001, India
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Israeli-Georgian Medical Research Clinic Healthycore, LTD
Tbilisi, 0112, Georgia
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Japanese Red Cross Osaka Hospital
Osaka, 543-8555, Japan
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Jordy Sinapse Medicina LTDA
Itapevi, São Paulo, 06655-250, Brazil
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Karadeniz Technical University Farabi Hospital
Trabzon, 61080, Turkey (Türkiye)
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Kasturba Medical College (KMC)
Udupi, Karnataka, 576104, India
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Kobe City Medical Center General Hospital
Kobe, Hyōgo, 650-0047, Japan
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Kocaeli University Hospital
Izmit, Van, 41380, Turkey (Türkiye)
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Kochi Medical School Hospital
Nankoku, Kochi, 783-8505, Japan
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Kyungpook National University Chilgok Hospital
Daegu, 41404, South Korea
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LTD National Center of Urology Named after L. Managadze
Tbilisi, 0144, Georgia
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LTD New Hospitals
Tbilisi, 0114, Georgia
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London Health Sciences Centre
London, Ontario, N6A 5A5, Canada
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Medical Hospital of Tokyo Medical and Dental University
Bunkyo, Tokyo, 113-8519, Japan
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Medsol Clinical Research Center Inc
Port Charlotte, Florida, 33952, United States
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Multiprofile Clinic Consilium Medulla
Tbilisi, 0186, Georgia
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NZOZ Neuro-kard
Poznan, Greater Poland Voivodeship, 61-853, Poland
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Nanfang Hospital Southern Medical University
Guangzhou, Guangdong, 510120, China
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National Cheng Kung University Hospital
Tainan, 701, Taiwan
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National Neuromuscular Research Institute
Austin, Texas, 78759, United States
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Nerve and Muscle Center of Texas
Houston, Texas, 77030, United States
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NeuroProtect
Warsaw, Mazovian, 01-684, Poland
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Neurological Services of Orlando
Orlando, Florida, 32806, United States
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Nihon University Itabashi Hospital
tabashi City, Tokyo, 173-8610, Japan
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Nizam's Institute of Medical Sciences (NIMS)
Panjagutta, Hyderabad, 500082, India
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NorthShore University Health System
Glenview, Illinois, 60026-1301, United States
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Northwest Neurology Ltd. - Clinedge - PPDS
Rolling Meadows, Illinois, 60080, United States
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Odense Universitetshospital
Odense, 05000, Denmark
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Okinawa National Hospital
Ginowan-Shi, Okinawa, 901-2214, Japan
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Okinawa Prefectural Nanbu Medical Center and Children's Medical Center
Shimajiri, Okinawa, 901-1193, Japan
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Ondokuz Mayis Universitesi Tip Fakultesi Hastanesi
Samsun, 55239, Turkey (Türkiye)
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Peking Union Medical College Hospital
Beijing, Beijing Municipality, 100032, China
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Penn Medicine University City
Philadelphia, Pennsylvania, 19104, United States
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Pineo Medical Ecosystem
Tbilisi, 0114, Georgia
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Polakulath Narayanan Renai Medicity Multi Specialty Hospital, Kochi
Kochi, Punjab, 141008, India
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Postgraduate Institute of Medical Education & Research
Chandigarh, 160012, India
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Pseg Centro de Pesquisa Clinica S.A
São Paulo, 04038-002, Brazil
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Qilu Hospital of Shandong University (Qingdan)
Qingdao, Shandong, 266035, China
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Renmin Hospital of Wuhan University - Hubei Provincial People's Hospital
Wuhan, Hubei, 430060, China
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Rigshospitalet, Copenhagen
Copenhagen, 2100, Denmark
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SFM Clinical Research, LLC
Boca Raton, Florida, 33487, United States
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Saitama Medical University, Saitama Medical Center
Kawagoe, Saitama, 350-8550, Japan
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Samsung Medical Center
Seoul, 06351, South Korea
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Seth G.S. Medical College & K.E.M. Hospital, Mumbai
Pārel, Mumbai, 400012, India
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Sheffield Teaching Hospital NHS Foundation Trust
Sheffield, South Yorkshire, 511 9NE, United Kingdom
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Shin Kong Wu Ho Su Memorial Hospital
Taipei, 111, Taiwan
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Sichuan Provincial People's Hospital
Chengdu, Sichuan, 610072, China
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St. Elizabeth's Hospital
O'Fallon, Illinois, 62269, United States
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The First Affiliated Hospital of Guangzhou University of Chinese Medicine
Guangzhou, Guangzhou, 510405, China
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The First Hospital of Jilin University
Changchun, Jilin, 130000, China
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The Second Affiliated Hospital of the Chinese Peoples' Liberation Army Air Force Medical University
Xi’an, Shanxi, 710032, China
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The University of Hong Kong-Shenzhen Hospital
Shenzhen, Guangdong, 518053, China
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Tianjin Medical University General Hospital
Tianjin, Tianjin Municipality, 300050, China
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Tokyo Medical University Hospital
Shinjuku, Tokyo, 160-0023, Japan
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Toronto General Hospital
Toronto, Ontario, M5G2C4, Canada
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Universita' Degli Studi di Roma La Sapienza
Roma, 00161, Italy
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Universitair Ziekenhuis Antwerpen
Edegem, Antwerp, 2650, Belgium
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Universitatsklinikum Jena
Jena, 07747, Germany
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Universitatsklinikum Leipzig
Leipzig, Saxony, 04103, Germany
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Universitatsklinikum Munster
Münster, North Rhine-Westphalia, 48149, Germany
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University Clinical Centre Nis
Niš, 700461, Serbia
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University Hospital Birmingham
Birmingham, B15 2TH, United Kingdom
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University Hospital Essen
Essen, North Rhine-Westphalia, 45127, Germany
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University of Alberta
Edmonton, Alberta, T6G 2X8, Canada
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University of California Irvine
Irvine, California, 92697, United States
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University of Cincinnati Gardner Neuroscience Institute
Cincinnati, Ohio, 45219, United States
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University of South Florida Morsani Center for Advanced Healthcare
Tampa, Florida, 33612, United States
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University of Southern California
Los Angeles, California, 90033, United States
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Uniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny
Warsaw, Mosavian, 02-097, Poland
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Wayne State University School of Medicine
Detroit, Michigan, 48201, United States
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Xiangya Hospital Central South University
Changsha, Hunan, 410008, China
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Yamaguchi University Hospital
Ube, Yamaguchi, 755-8505, Japan
Conditions
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