New drug combo aims to tame debilitating muscle disease

NCT ID NCT05070858

Summary

This study is testing two new drugs, pozelimab and cemdisiran, to see if they can better control the muscle weakness and fatigue caused by generalized myasthenia gravis (gMG). It will involve about 288 adults with gMG to compare the effectiveness and safety of using the drugs together versus using cemdisiran alone. The main goal is to see if the treatments can help patients perform daily activities more easily.

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Contacts and locations

Locations

  • AZ Sint-Lucas

    Ghent, Oost-Vlaanderen, 9000, Belgium

  • Aalborg Universitetshospital

    Aalborg, North Denmark, 09000, Denmark

  • Aarhus University Hospital

    Aarhus N, 8200, Denmark

  • All India Institute of Medical Sciences New Delhi

    New Delhi, National Capital Territory of Delhi, 110029, India

  • Amrita Institute of Medical Sciences and Research Centre (AIMS)

    Kochi, Kerala, 682041, India

  • Apex Hospital

    Jaipur, Rajasthan, 302017, India

  • Aqualane Clinical Research

    Naples, Florida, 34105, United States

  • Azienda Ospedaliera Papa Giovanni XXIII

    Bergamo, 24127, Italy

  • Azienda Ospedaliera Sant'andrea

    Rome, Lazio, 00189, Italy

  • Azienda Ospedaliero Universitaria Pisana

    Pisa, Tuscany, 56126, Italy

  • Bangalore Medical College and Research Institute (BMCRI) - Victoria Hospital

    Bangalore, 560002, India

  • CHU Bicetre

    Le Kremlin-Bicêtre, 94275, France

  • Centre Hospitalier Regional Universitaire (CHRU) de Nancy

    Nancy, 54035, France

  • Centre Hospitalier Universitaire de Nice

    Nice, Alpes Maritimes, 6002, France

  • Centrum Neurologii Klinicznej, Krakowska Akademia Neurologii

    Krakow, Lesser Poland Voivodeship, 31-505, Poland

  • Chang Gung Memorial Foundation Kaohsiung Branch

    Kaohsiung City, 833, Taiwan

  • Chang Gung Memorial Hospital at Linkou

    Taoyuan District, 333, Taiwan

  • Charite - Universitatsmedizin Berlin

    Berlin, 10117, Germany

  • Chiba University Hospital

    Chiba, 260-8677, Japan

  • China Medical University

    Taichung, 40447, Taiwan

  • Christian Medical College & Hospital

    Ludhiana, Punjab, 141008, India

  • City Neuro Centre, Hyderabad

    Hyderabad, Telangana, 500034, India

  • Clinical Research Center Spolka z Ograniczona Odpowiedzialnoscia Medic-R Sp.k

    Poznan, Greater Poland Voivodeship, 61-731, Poland

  • Colorado Springs Neurological Associates

    Colorado Springs, Colorado, 80907-5307, United States

  • Dayton Center for Neurological Disorders

    Centerville, Ohio, 45459, United States

  • Deenanath Mangeshkar Hospital and Research Centre

    Pune, Maharashtra, 411004, India

  • Diverse Clinical Research

    Miami, Florida, 33175, United States

  • Dokuz Eylul University Medical Faculty

    Izmir, 35340, Turkey (Türkiye)

  • Faculdade de Medicina Do ABC

    Santo André, São Paulo, 09060-870, Brazil

  • Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta

    Milan, Lombardy, 20133, Italy

  • Friedrich Baur Institute

    München, Bavaria, 80336, Germany

  • Fujian Medical University Union Hospital

    Fuzhou, Fujian, 350001, China

  • Gdanski Uniwersytet Medyczny

    Gdansk, Pomeranian Voivodeship, 80-952, Poland

  • Government General Hospital, Guntur

    Guntur, Andhra Pradesh, 522001, India

  • Guangdong Hospital of Traditional Chinese Medicine

    Guangdong, Guangdong, 510120, China

  • Hainan General Hospital

    Haikou, Hainan, 570311, China

  • Hiroshima City Hiroshima Citiz

    Hiroshima, 730-8518, Japan

  • HonorHealth Neurology 2018

    Scottsdale, Arizona, 85251, United States

  • Hopital de la Pitie Salpetriere

    Paris, 75013, France

  • Hospital Universitari i Politecnic La Fe

    Valencia, 46026, Spain

  • Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo

    São Paulo, 05403-010, Brazil

  • Hospital de la Santa Creu i Sant Pau

    Barcelona, 08041, Spain

  • Huashan Hospital Fudan University

    Shanghai, Shanghai Municipality, 201107, China

  • IMV Pesquisa Neurologica

    Porto Alegre, Rio Grande do Sul, 90110-000, Brazil

  • Institute of Neurosciences

    Surat, Gujarat, 395001, India

  • Israeli-Georgian Medical Research Clinic Healthycore, LTD

    Tbilisi, 0112, Georgia

  • Japanese Red Cross Osaka Hospital

    Osaka, 543-8555, Japan

  • Jordy Sinapse Medicina LTDA

    Itapevi, São Paulo, 06655-250, Brazil

  • Karadeniz Technical University Farabi Hospital

    Trabzon, 61080, Turkey (Türkiye)

  • Kasturba Medical College (KMC)

    Udupi, Karnataka, 576104, India

  • Kobe City Medical Center General Hospital

    Kobe, Hyōgo, 650-0047, Japan

  • Kocaeli University Hospital

    Izmit, Van, 41380, Turkey (Türkiye)

  • Kochi Medical School Hospital

    Nankoku, Kochi, 783-8505, Japan

  • Kyungpook National University Chilgok Hospital

    Daegu, 41404, South Korea

  • LTD National Center of Urology Named after L. Managadze

    Tbilisi, 0144, Georgia

  • LTD New Hospitals

    Tbilisi, 0114, Georgia

  • London Health Sciences Centre

    London, Ontario, N6A 5A5, Canada

  • Medical Hospital of Tokyo Medical and Dental University

    Bunkyo, Tokyo, 113-8519, Japan

  • Medsol Clinical Research Center Inc

    Port Charlotte, Florida, 33952, United States

  • Multiprofile Clinic Consilium Medulla

    Tbilisi, 0186, Georgia

  • NZOZ Neuro-kard

    Poznan, Greater Poland Voivodeship, 61-853, Poland

  • Nanfang Hospital Southern Medical University

    Guangzhou, Guangdong, 510120, China

  • National Cheng Kung University Hospital

    Tainan, 701, Taiwan

  • National Neuromuscular Research Institute

    Austin, Texas, 78759, United States

  • Nerve and Muscle Center of Texas

    Houston, Texas, 77030, United States

  • NeuroProtect

    Warsaw, Mazovian, 01-684, Poland

  • Neurological Services of Orlando

    Orlando, Florida, 32806, United States

  • Nihon University Itabashi Hospital

    tabashi City, Tokyo, 173-8610, Japan

  • Nizam's Institute of Medical Sciences (NIMS)

    Panjagutta, Hyderabad, 500082, India

  • NorthShore University Health System

    Glenview, Illinois, 60026-1301, United States

  • Northwest Neurology Ltd. - Clinedge - PPDS

    Rolling Meadows, Illinois, 60080, United States

  • Odense Universitetshospital

    Odense, 05000, Denmark

  • Okinawa National Hospital

    Ginowan-Shi, Okinawa, 901-2214, Japan

  • Okinawa Prefectural Nanbu Medical Center and Children's Medical Center

    Shimajiri, Okinawa, 901-1193, Japan

  • Ondokuz Mayis Universitesi Tip Fakultesi Hastanesi

    Samsun, 55239, Turkey (Türkiye)

  • Peking Union Medical College Hospital

    Beijing, Beijing Municipality, 100032, China

  • Penn Medicine University City

    Philadelphia, Pennsylvania, 19104, United States

  • Pineo Medical Ecosystem

    Tbilisi, 0114, Georgia

  • Polakulath Narayanan Renai Medicity Multi Specialty Hospital, Kochi

    Kochi, Punjab, 141008, India

  • Postgraduate Institute of Medical Education & Research

    Chandigarh, 160012, India

  • Pseg Centro de Pesquisa Clinica S.A

    São Paulo, 04038-002, Brazil

  • Qilu Hospital of Shandong University (Qingdan)

    Qingdao, Shandong, 266035, China

  • Renmin Hospital of Wuhan University - Hubei Provincial People's Hospital

    Wuhan, Hubei, 430060, China

  • Rigshospitalet, Copenhagen

    Copenhagen, 2100, Denmark

  • SFM Clinical Research, LLC

    Boca Raton, Florida, 33487, United States

  • Saitama Medical University, Saitama Medical Center

    Kawagoe, Saitama, 350-8550, Japan

  • Samsung Medical Center

    Seoul, 06351, South Korea

  • Seth G.S. Medical College & K.E.M. Hospital, Mumbai

    Pārel, Mumbai, 400012, India

  • Sheffield Teaching Hospital NHS Foundation Trust

    Sheffield, South Yorkshire, 511 9NE, United Kingdom

  • Shin Kong Wu Ho Su Memorial Hospital

    Taipei, 111, Taiwan

  • Sichuan Provincial People's Hospital

    Chengdu, Sichuan, 610072, China

  • St. Elizabeth's Hospital

    O'Fallon, Illinois, 62269, United States

  • The First Affiliated Hospital of Guangzhou University of Chinese Medicine

    Guangzhou, Guangzhou, 510405, China

  • The First Hospital of Jilin University

    Changchun, Jilin, 130000, China

  • The Second Affiliated Hospital of the Chinese Peoples' Liberation Army Air Force Medical University

    Xi’an, Shanxi, 710032, China

  • The University of Hong Kong-Shenzhen Hospital

    Shenzhen, Guangdong, 518053, China

  • Tianjin Medical University General Hospital

    Tianjin, Tianjin Municipality, 300050, China

  • Tokyo Medical University Hospital

    Shinjuku, Tokyo, 160-0023, Japan

  • Toronto General Hospital

    Toronto, Ontario, M5G2C4, Canada

  • Universita' Degli Studi di Roma La Sapienza

    Roma, 00161, Italy

  • Universitair Ziekenhuis Antwerpen

    Edegem, Antwerp, 2650, Belgium

  • Universitatsklinikum Jena

    Jena, 07747, Germany

  • Universitatsklinikum Leipzig

    Leipzig, Saxony, 04103, Germany

  • Universitatsklinikum Munster

    Münster, North Rhine-Westphalia, 48149, Germany

  • University Clinical Centre Nis

    Niš, 700461, Serbia

  • University Hospital Birmingham

    Birmingham, B15 2TH, United Kingdom

  • University Hospital Essen

    Essen, North Rhine-Westphalia, 45127, Germany

  • University of Alberta

    Edmonton, Alberta, T6G 2X8, Canada

  • University of California Irvine

    Irvine, California, 92697, United States

  • University of Cincinnati Gardner Neuroscience Institute

    Cincinnati, Ohio, 45219, United States

  • University of South Florida Morsani Center for Advanced Healthcare

    Tampa, Florida, 33612, United States

  • University of Southern California

    Los Angeles, California, 90033, United States

  • Uniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny

    Warsaw, Mosavian, 02-097, Poland

  • Wayne State University School of Medicine

    Detroit, Michigan, 48201, United States

  • Xiangya Hospital Central South University

    Changsha, Hunan, 410008, China

  • Yamaguchi University Hospital

    Ube, Yamaguchi, 755-8505, Japan

Conditions

Explore the condition pages connected to this study.