Race against time: new drug trial aims to slow devastating brain disease
NCT ID NCT06706622
Summary
This large, late-stage trial is testing whether a new drug called amlenetug can slow down the progression of multiple system atrophy (MSA), a rare and serious brain disorder. About 357 people with MSA will receive either the drug or a placebo via monthly IV infusions for over a year, with the option to continue on the drug afterward. The main goal is to see if the treatment can delay worsening of symptoms and improve survival.
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Contacts and locations
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Locations
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A.O.U. Pisana-Ospedale S. Chiara
Pisa, 56126, Italy
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AOU Universita della Campania Luigi Vanvitelli
Naples, 80138, Italy
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Baylor College Of Medicine
Houston, Texas, 77030, United States
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Beth Israel Deaconess Medical Center
Boston, Massachusetts, 02215, United States
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Brigham and Women's Hospital
Boston, Massachusetts, 02115, United States
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CHU - Hospital de la Timone
Marseille, 13385, France
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CenExel Rocky Mountain Clinical Research, LLC
Englewood, Colorado, 80113, United States
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Centre Hospitalier Regional Universitaire (CHRU) Montpellier - Hopital Saint-Eloi Guy de Chauliac
Montpellier, 34295, France
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Centre Hospitalier Regional Universitaire de Lille - Hopital Roger Salengro
Lille, 59037, France
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Centre Hospitalier Universitaire (CHU) de Bordeaux - Groupe Hospitalier Pellegrin
Bordeaux, 33076, France
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Centre Hospitalier Universitaire de Toulouse - Hopital Purpan
Toulouse, 31059, France
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Chu De La Pitie-Salpetriere
Paris, 75651, France
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Cleveland Clinic - Neurological Institute
Cleveland, Ohio, 44195, United States
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Clinical Ageing Reseach Unit
Newcastle upon Tyne, Tyne and Wear, NE4 5LP, United Kingdom
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Columbia University Medical Center - The Neurological Institute of New York
New York, New York, 10032-3726, United States
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Curiositas-ad-sanum Beratungs-und Studien GmbH
Haag in Oberbayern, 83527, Germany
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Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico
Milan, 20122, Italy
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Fondazione IRCCS Istituto Neurologico Carlo Besta
Milan, 20133, Italy
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Fujita Health University Hospital
Toyoake, Aichi-ken, 470-1192, Japan
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Gifu University Hospital
Gifu, Gifu, 501-1194, Japan
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Gold Coast Hospital
Southport, Queensland, 4215, Australia
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Hokkaido University Hospital
Sapporo, Hokkaido, 060-8648, Japan
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Hospital Clinic de Barcelona - Institut Clinic de Neurociencies (ICN)
Barcelona, 08036, Spain
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Hospital Universitario Vall d'Hebron
Barcelona, 08035, Spain
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Hospital Universitario Virgen del Rocio (HUVR) - Instituto de Biomedicina de Sevilla (IBIS)
Seville, 41015, Spain
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Hospital Universitario de La Princesa
Madrid, 28006, Spain
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Hospital de la Santa Creu i Sant Pau
Barcelona (Spain), 08041, Spain
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IRCCS Institute of Neurological Sciences of Bologna- Universita di Bologna
Bologna, 40139, Italy
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Indiana Health University
Indianapolis, Indiana, 46202, United States
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Inland Northwest Research
Spokane, Washington, 99202, United States
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Johns Hopkins University School of Medicine
Baltimore, Maryland, 21287, United States
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Juntendo University Hospital
Bunkyo-ku, Tokyo, 113-8431, Japan
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Keio University Hospital
Tokyo, 160-8582, Japan
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Kyung Hee University Hospital
Seoul, 02447, South Korea
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Liverpool Hospital - South Western Sydney Local Health District
Liverpool, New South Wales, 2170, Australia
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Ludwig-Maximilians-Universitat Munchen Klinikum der Universitat - Grosshadern
München, 81377, Germany
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Mayo Clinic
Scottsdale, Arizona, 85259, United States
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Mayo Clinic
Rochester, Minnesota, 55905, United States
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Movement Disorders Clinic
Beelitz-Heilstätten, 14547, Germany
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NYU Medical Center - Dysautonomia center
New York, New York, 10016, United States
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National Center Hospital, National Center of Neurology and Psychiatry
Kodaira-shi, Tokyo, 187-8551, Japan
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National Hospital Organization Higashinagoya National Hospital
Nagoya, Aichi-ken, 465-8620, Japan
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National Hospital Organization Sendai Nishitaga Hospital
Sendai, Miyagi, 982-8555, Japan
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Niigata University Medical And Dental Hospital
Niigata, 9518520, Japan
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Nuffield Oxford University and Oxford University Hospital NHS Foundation Trusts-John Radcliffe Ho...
Oxford, Oxfordshire, OX3 9DU, United Kingdom
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Parkinson's Disease And Movement Disorder Center Of Boca Raton
Boca Raton, Florida, 33486, United States
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QUEST Research Institute
Farmington Hills, Michigan, 48334, United States
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Queen Elizabeth University Hospital - NHS Greater Glasgow & Clyde
Glasgow, Scotland, G51 4TF, United Kingdom
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Royal Devon and Exeter Hospital - Royal Devon University Healthcare NHS Foundation Trust
Exeter, EX2 5DW, United Kingdom
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Saitama Medical University Hospital
Iruma-gun, 350-0495, Japan
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Salford Royal Hospital, Northern Care Alliance NHS Foundation Trust
Salford, Greater Manchester, M6 8HD, United Kingdom
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Samsung Medical Center
Seoul, 06351, South Korea
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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The Alfred Hospital
Melbourne, Victoria, 3004, Australia
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The National Hospital for Neurology and Neurosurgery
London, WC1N 3BG, United Kingdom
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The Ottawa Hospital Research Institute
Ottawa, Ontario, K1H 8L6, Canada
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Toronto Western Hospital (TWH)
Toronto, Ontario, M5T 2S8, Canada
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Tottori University Hospital
Yonago-shi, Tottori, 683-8504, Japan
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Unite d'investigation clinique de Neurologie Rez-de-jardin-Bloc Hopital CHU Pontchaillou
Rennes, 35033, France
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Universita Di Salerno Aou San Giovanni Di Dio E Ruggi D'Aragona
Salerno, 84100, Italy
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Universitaetsklinikum Erlangen
Erlangen, 91054, Germany
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Universitaetsklinikum Muenster
Münster, 48149, Germany
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Universitat de Valencia - Hospital Universitari i Politecnic La Fe de Valencia (Hospital La Fe Bu...
Valencia, 46026, Spain
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University Hospital Tuebingen
Tübingen, 72076, Germany
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University Nebraska Medical Center
Omaha, Nebraska, 68198-8440, United States
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University Of Pittsburgh
Pittsburgh, Pennsylvania, 15213, United States
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University of Arkansas for Medical Sciences
Little Rock, Arkansas, 72205, United States
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University of California, San Francisco Neurosciences Clinical Research Unit
San Francisco, California, 94158, United States
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University of Florida Norman Fixel Institute for Neurological Diseases
Gainesville, Florida, 32608, United States
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University of Pennsylvania
Philadelphia, Pennsylvania, 19107, United States
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University of Texas Southwestern Medical Center ¿ Multiple System Atrophy Clinic
Dallas, Texas, 75390-8565, United States
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Vanderbilt University Medical Center-Cognitive and Movement Disorders Group
Nashville, Tennessee, 37232, United States
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Westmead Hospital
Westmead, New South Wales, 2145, Australia
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Yale New Haven Health
North Haven, Connecticut, 06473, United States
Conditions
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