New study aims to unlock secrets of rare bone disease without surgery

NCT ID NCT05284006

First seen May 14, 2026 · Last updated May 15, 2026 · Updated 2 times

Summary

This study is for people with Morquio A, a rare disease that affects bones and breathing. Researchers want to learn more about how the disease progresses by using safe, non-invasive tests like X-rays, MRIs, and breathing tests. The goal is to find better ways to measure the disease, which could help design future treatments. About 60 participants will be followed over time.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Nemours Children's Health, Delaware Valley

    RECRUITING

    Wilmington, Delaware, 19803, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.