New drug ML-004 moves to safety testing in autism patients

NCT ID NCT05889273

First seen Jun 27, 2026 · Last updated Jul 21, 2026 · Updated 2 times

Summary

This study is testing the safety of an experimental drug called ML-004 in 120 adolescents and adults with autism spectrum disorder who have already completed a previous study. Participants will take ML-004 once daily, and researchers will monitor for side effects. The goal is to see if the drug is safe enough for further testing.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
ML-004 tablet
What this could lead to
If it works, this could point toward a treatment to help manage core symptoms of autism spectrum disorder.
What could go wrong
This is an early-phase safety study, so it is not designed to prove effectiveness. The drug may cause side effects or not work better than a placebo.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • APG Research, LLC

    Orlando, Florida, 32803, United States

  • Abba Medical Group

    Miami, Florida, 33176, United States

  • BioBehavioral Research of Austin

    Austin, Texas, 78759, United States

  • Brain and Mind Centre

    Camperdown, New South Wales, 2050, Australia

  • Cortica

    San Rafael, California, 94903, United States

  • Cortica Healthcare

    Glendale, California, 91203, United States

  • Family Psychiatry of The Woodlands

    The Woodlands, Texas, 77381, United States

  • Harmonex Neuroscience Research

    Dothan, Alabama, 36303, United States

  • Holland Bloorview Kids Rehabilitation Hospital

    Toronto, Ontario, M4G 1R8, Canada

  • NRC Research Institute

    Orange, California, 92868, United States

  • Nathan Kline Institute for Psychiatric Research

    Orangeburg, New York, 10962, United States

  • Neurobehavioral Medicine Group

    Bloomfield Hills, Michigan, 48302, United States

  • Richmond Behavioral Associates

    Staten Island, New York, 10314, United States

  • Road Runner Research, Ltd.

    San Antonio, Texas, 78249, United States

  • Southwest Autism Research and Resource Center

    Phoenix, Arizona, 85006, United States

  • Suburban Research Associates

    Media, Pennsylvania, 19063, United States

  • The Children's Research Institute

    Washington D.C., District of Columbia, 20010, United States

  • The Royal Children's Hospital, Murdoch Children's Research Institute

    Parkville, Victoria, 3052, Australia

  • University of Missouri, Thompson Center for Autism & Neurodevelopment

    Columbia, Missouri, 65211, United States

  • University of South Florida Psychiatry and Behavioral Neurosciences

    Tampa, Florida, 33613, United States

  • Yale Child Study Center

    New Haven, Connecticut, 06519, United States

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