New drug trial offers hope for kids with rare, dangerous blood disease

NCT ID NCT06153173

Summary

This study is testing an oral drug called mirdametinib for people with rare histiocytic disorders like Langerhans Cell Histiocytosis (LCH). It aims to see if this targeted treatment works better and has fewer side effects than current chemotherapy, especially for patients whose disease affects vital organs. The trial will enroll about 40 participants aged 2 and older who need systemic treatment.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.