New injection could transform bleed prevention for kids with haemophilia

NCT ID NCT05306418

Summary

This study tested a new preventative medicine called Mim8 in children aged 1-11 with haemophilia A. Mim8 is given as a shot under the skin to try to prevent bleeding episodes. The trial compared Mim8 to other standard treatments to see if it was safe, effective, and easier for families to manage.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • A.O.U. Città della Salute e della Scienza di Torino-Ospedale

    Torino, 10126, Italy

  • Academisch Medisch Centrum

    Amsterdam, 1105 AZ, Netherlands

  • Arthur Bloom Haemophilia Centre

    Cardiff, CF14 4XW, United Kingdom

  • Beijing Children's Hospital, Capital Medical University

    Beijing, Beijing Municipality, 100045, China

  • Beijing Children's Hospital,Capital Medical University

    Beijing, Beijing Municipality, 100045, China

  • CSK UM Uniwersyteckie Centrum Pediatrii im. M. Konopnickiej

    Lodz, 91-738, Poland

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Chengdu Women's and Children's Central Hospital

    Chengdu, Sichuan, 610000, China

  • Children Oncohaematology department Children's Hospital,

    Vilnius, 08406, Lithuania

  • Children Regional Clinical Hospital

    Krasnodar, 350007, Russia

  • Children's Healthcare Atlanta

    Atlanta, Georgia, 30322, United States

  • Children's Hospital Los Angeles - Endocrinology

    Los Angeles, California, 90027, United States

  • Children's Hospital at Memorial Health

    Savannah, Georgia, 31404, United States

  • Children's Hospital, Zhejiang University School of Medicine

    Hangzhou, Zhejiang, 310052, China

  • Daejeon Eulji Medical Center, Eulji University

    Daejeon, 35233, South Korea

  • Hospital Sant Joan de Déu

    Esplugues Llobregat, 08950, Spain

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Institute of Hematology and Blood Diseases Hospital, Tianjin-Hematology

    Tianjin, Tianjin Municipality, 300020, China

  • J K Lon Hospital

    Jaipur, Rajasthan, 302004, India

  • McMaster Children's Hospital

    Hamilton, Ontario, L8N 3Z5, Canada

  • Morozovskaya municipal children hospital

    Moscow, 119049, Russia

  • Nanfang Hospital, Southern Medical University-Haematology

    Guangzhou, Guangdong, 510515, China

  • National Taiwan University Children's Hospital

    Taipei, 100, Taiwan

  • Nirmal Hospital Pvt. Ltd.

    Surat, Gujarat, 395002, India

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Ospedale Pediatrico Bambino Ges

    Rome, 00165, Italy

  • Ota Memorial Hospital_Pediatrics

    Gunma, 373-8585, Japan

  • Penn State MS Hershey Med Ctr

    Hershey, Pennsylvania, 17033-2360, United States

  • Post Graduate Institute of Child Health

    Noida, Uttar Pradesh, 201303, India

  • Pädiatrische Onkologie-Hämatologie

    Lucerne, 6000, Switzerland

  • Republican Hospital n.a. V. A. Baranov

    Petrozavodsk, 185019, Russia

  • SAHI Kuzbass Hospital(former Regional clinical hospital)

    Kemerovo, 650066, Russia

  • Sahyadri Super Speciality Hospital

    Pune, Maharashtra, 411004, India

  • Saitama Children's Med Centre_Hematology-Oncology

    Saitama, 330-8777, Japan

  • Sapporo Tokushukai Hospital_Pediatrics

    Hokkaido, 004-0041, Japan

  • Seth GS Medical College & KEM Hospital

    Mumbai, Maharashtra, 400012, India

  • Severance Hospital, Yonsei University Health System

    Seoul, 03722, South Korea

  • Sheba MC - The Israeli National Hemophilia Center

    Tel Litwinsky, 52621, Israel

  • St Christopher Hosp for Child

    Philadelphia, Pennsylvania, 19134, United States

  • St Joseph's Hospital Foundation

    Tampa, Florida, 33607, United States

  • St Thomas' Hospital - Haemostasis and Thrombosis Centre

    London, SE1 7EH, United Kingdom

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • ULS São João, E.P.E.

    Porto, 4200-319, Portugal

  • UMC Utrecht, Van Creveldkliniek

    Utrecht, 3584 CX, Netherlands

  • Unidade Local de Saúde São José EPE- Hospital D. Estefânia

    Lisbon, 1169-045, Portugal

  • Univ Hosp Cleveland Med Ctr

    Cleveland, Ohio, 44106, United States

  • Univ of Colorado Sch of Med

    Aurora, Colorado, 80045, United States

  • University of Iowa_Iowa City

    Iowa City, Iowa, 52242, United States

  • Universitätsklinik für Kinderheilkunde

    Bern, 3010, Switzerland

  • Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie

    Bonn, 53127, Germany

  • Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa

    Lublin, 20-093, Poland

  • Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego

    Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

Conditions

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